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The 4-Copy Conundrum in the Treatment of Infants with Spinal Muscular Atrophy.
Deng, Stella; Lee, Bo Hoon; Ciafaloni, Emma; Mackenzie, Samuel J.
Afiliação
  • Deng S; Division of Child Neurology, Department of Neurology, University of Rochester, Rochester, New York, USA.
  • Lee BH; Division of Child Neurology, Department of Neurology, University of Rochester, Rochester, New York, USA.
  • Ciafaloni E; Division of Neuromuscular Disease, Department of Neurology, University of Rochester, Rochester, New York, USA.
  • Mackenzie SJ; Division of Neuromuscular Disease, Department of Neurology, University of Rochester, Rochester, New York, USA.
Ann Neurol ; 91(6): 891, 2022 06.
Article em En | MEDLINE | ID: mdl-35338521

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Atrofia Muscular Espinal / Atrofias Musculares Espinais da Infância Limite: Humans / Infant Idioma: En Ano de publicação: 2022 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Atrofia Muscular Espinal / Atrofias Musculares Espinais da Infância Limite: Humans / Infant Idioma: En Ano de publicação: 2022 Tipo de documento: Article