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Delivery and assessment of a CRISPR/nCas9-based genome editing system on in vitro models of mucopolysaccharidoses IVA assisted by magnetite-based nanoparticles.
Leal, Andrés Felipe; Cifuentes, Javier; Torres, Carlos Emilio; Suárez, Diego; Quezada, Valentina; Gómez, Saúl Camilo; Cruz, Juan C; Reyes, Luis H; Espejo-Mojica, Angela Johana; Alméciga-Díaz, Carlos Javier.
Afiliação
  • Leal AF; Institute for the Study of Inborn Errors of Metabolism, Faculty of Science, Pontificia Universidad Javeriana, Cra. 7 No. 43-82 Building 54, Room 305A, 110231, Bogotá D.C., Colombia.
  • Cifuentes J; Department of Biomedical Engineering, Universidad de los Andes, 111711, Bogotá, Colombia.
  • Torres CE; Department of Biomedical Engineering, Universidad de los Andes, 111711, Bogotá, Colombia.
  • Suárez D; Institute for the Study of Inborn Errors of Metabolism, Faculty of Science, Pontificia Universidad Javeriana, Cra. 7 No. 43-82 Building 54, Room 305A, 110231, Bogotá D.C., Colombia.
  • Quezada V; Department of Biomedical Engineering, Universidad de los Andes, 111711, Bogotá, Colombia.
  • Gómez SC; Department of Biomedical Engineering, Universidad de los Andes, 111711, Bogotá, Colombia.
  • Cruz JC; Department of Biomedical Engineering, Universidad de los Andes, 111711, Bogotá, Colombia.
  • Reyes LH; Grupo de Diseño de Productos y Procesos (GDPP), Department of Chemical and Food Engineering, Universidad de los Andes, 111711, Bogotá, Colombia.
  • Espejo-Mojica AJ; Institute for the Study of Inborn Errors of Metabolism, Faculty of Science, Pontificia Universidad Javeriana, Cra. 7 No. 43-82 Building 54, Room 305A, 110231, Bogotá D.C., Colombia.
  • Alméciga-Díaz CJ; Institute for the Study of Inborn Errors of Metabolism, Faculty of Science, Pontificia Universidad Javeriana, Cra. 7 No. 43-82 Building 54, Room 305A, 110231, Bogotá D.C., Colombia. cjalmeciga@javeriana.edu.co.
Sci Rep ; 12(1): 15045, 2022 09 03.
Article em En | MEDLINE | ID: mdl-36057729

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Condroitina Sulfatases / Mucopolissacaridoses / Mucopolissacaridose IV / Nanopartículas Limite: Humans Idioma: En Ano de publicação: 2022 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Condroitina Sulfatases / Mucopolissacaridoses / Mucopolissacaridose IV / Nanopartículas Limite: Humans Idioma: En Ano de publicação: 2022 Tipo de documento: Article