Correction of DMD in human iPSC-derived cardiomyocytes by base-editing-induced exon skipping.

Wang, Peipei; Li, Haiwen; Zhu, Mandi; Han, Rena Y; Guo, Shuliang; Han, Renzhi.

Afiliação

Wang P; Department of Surgery, Davis Heart and Lung Research Institute, Biomedical Sciences Graduate Program, Biophysics Graduate Program, The Ohio State University Wexner Medical Center, Columbus, OH 43210, USA.
Li H; Department of Surgery, Davis Heart and Lung Research Institute, Biomedical Sciences Graduate Program, Biophysics Graduate Program, The Ohio State University Wexner Medical Center, Columbus, OH 43210, USA.
Zhu M; Department of Surgery, Davis Heart and Lung Research Institute, Biomedical Sciences Graduate Program, Biophysics Graduate Program, The Ohio State University Wexner Medical Center, Columbus, OH 43210, USA.
Han RY; Olentangy Liberty High School, Powell, OH 43065, USA.
Guo S; Department of Surgery, Davis Heart and Lung Research Institute, Biomedical Sciences Graduate Program, Biophysics Graduate Program, The Ohio State University Wexner Medical Center, Columbus, OH 43210, USA.
Han R; Department of Surgery, Davis Heart and Lung Research Institute, Biomedical Sciences Graduate Program, Biophysics Graduate Program, The Ohio State University Wexner Medical Center, Columbus, OH 43210, USA.

Mol Ther Methods Clin Dev ; 28: 40-50, 2023 Mar 09.

Article em En | MEDLINE | ID: mdl-36588820