Cardiovascular Research in Friedreich Ataxia: Unmet Needs and Opportunities.
JACC Basic Transl Sci
; 7(12): 1267-1283, 2022 Dec.
Article
em En
| MEDLINE
| ID: mdl-36644283
CMR, cardiac magnetic resonance; FDA, U.S. Food and Drug Administration; FRDA, Friedreich ataxia; Friedreich ataxia; GAA, triplet expansion in first intron of the Friedreich ataxia gene; HF, heart failure; LV, left ventricle; LVEF, left ventricular ejection fraction; LVMI, left ventricular mass index; RV, right ventricle; cardiomyopathy; frataxin; heart; mitochondria
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2022
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