Comparing ability and norm-referenced scores as clinical trial outcomes for neurodevelopmental disabilities: a simulation study.

Farmer, Cristan; Thurm, Audrey; Troy, Jesse D; Kaat, Aaron J

Farmer, Cristan; Thurm, Audrey; Troy, Jesse D; Kaat, Aaron J.

Afiliação

Farmer C; Neurodevelopmental and Behavioral Phenotyping Service, National Institute of Mental Health, Bethesda, MD, USA. farmerca@mail.nih.gov.
Thurm A; Neurodevelopmental and Behavioral Phenotyping Service, National Institute of Mental Health, Bethesda, MD, USA.
Troy JD; Department of Biostatistics and Bioinformatics, Duke University School of Medicine, Durham, NC, USA.
Kaat AJ; Feinberg School of Medicine, Northwestern University, Chicago, IL, USA.

J Neurodev Disord ; 15(1): 4, 2023 01 17.

Article em En | MEDLINE | ID: mdl-36650450

Assuntos

Transtornos do Neurodesenvolvimento; Humanos; Comunicação; Aprendizagem; Transtornos do Neurodesenvolvimento/diagnóstico; Simulação de Paciente

Palavras-chave

Ability score; Clinical outcome assessment; Clinical trials; Endpoints; Floor effect; Growth scale value; Item response theory; Neurodevelopmental disability; Rare genetic condition; Rasch analysis

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Texto completo: 1 Base de dados: MEDLINE Assunto principal: Transtornos do Neurodesenvolvimento Tipo de estudo: Diagnostic_studies / Prognostic_studies Limite: Humans Idioma: En Ano de publicação: 2023 Tipo de documento: Article

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