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Emicizumab in people with moderate or mild haemophilia A (HAVEN 6): a multicentre, open-label, single-arm, phase 3 study.
Négrier, Claude; Mahlangu, Johnny; Lehle, Michaela; Chowdary, Pratima; Catalani, Olivier; Bernardi, Ronald J; Jiménez-Yuste, Víctor; Beckermann, Benjamin M; Schmitt, Christophe; Ventriglia, Giuliana; Windyga, Jerzy; d'Oiron, Roseline; Moorehead, Paul; Koparkar, Sunita; Teodoro, Vanda; Shapiro, Amy D; Oldenburg, Johannes; Hermans, Cedric.
Afiliação
  • Négrier C; Claude Bernard Lyon 1 University, Lyon, France. Electronic address: claude.negrier@univ-lyon1.fr.
  • Mahlangu J; University of the Witwatersrand and NHLS, Johannesburg, South Africa.
  • Lehle M; F Hoffmann-La Roche, Basel, Switzerland.
  • Chowdary P; Katharine Dormandy Haemophilia and Thrombosis Centre, Royal Free London, London, UK.
  • Catalani O; F Hoffmann-La Roche, Basel, Switzerland.
  • Bernardi RJ; Genentech, San Francisco, CA, USA.
  • Jiménez-Yuste V; La Paz University Hospital, Autonomous University of Madrid, Madrid, Spain.
  • Beckermann BM; F Hoffmann-La Roche, Basel, Switzerland.
  • Schmitt C; F Hoffmann-La Roche, Basel, Switzerland.
  • Ventriglia G; F Hoffmann-La Roche, Basel, Switzerland.
  • Windyga J; Department of Hemostasis Disorders and Internal Medicine, Laboratory of Hemostasis and Metabolic Diseases, Institute of Hematology and Transfusion Medicine, Warsaw, Poland.
  • d'Oiron R; Bicêtre Hospital AP-HP, University of Paris-Saclay and UMR_S1176 INSERM, Le Kremlin-Bicêtre, Paris, France.
  • Moorehead P; Memorial University of Newfoundland, St John's, NL, Canada.
  • Koparkar S; Genentech, San Francisco, CA, USA.
  • Teodoro V; F Hoffmann-La Roche, Basel, Switzerland.
  • Shapiro AD; Indiana Hemophilia and Thrombosis Center, Indianapolis, IN, USA.
  • Oldenburg J; Institute of Experimental Haematology and Transfusion Medicine, University of Bonn, Bonn, Germany.
  • Hermans C; University Clinic of Saint Luke, Catholic University of Louvain, Brussels, Belgium.
Lancet Haematol ; 10(3): e168-e177, 2023 Mar.
Article em En | MEDLINE | ID: mdl-36716761

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Anticorpos Biespecíficos / Microangiopatias Trombóticas / Hemofilia A Tipo de estudo: Clinical_trials Limite: Adult / Female / Humans / Male Idioma: En Ano de publicação: 2023 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Anticorpos Biespecíficos / Microangiopatias Trombóticas / Hemofilia A Tipo de estudo: Clinical_trials Limite: Adult / Female / Humans / Male Idioma: En Ano de publicação: 2023 Tipo de documento: Article