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Efficacy and safety of emapalumab in macrophage activation syndrome.
De Benedetti, Fabrizio; Grom, Alexei A; Brogan, Paul A; Bracaglia, Claudia; Pardeo, Manuela; Marucci, Giulia; Eleftheriou, Despina; Papadopoulou, Charalampia; Schulert, Grant S; Quartier, Pierre; Antón, Jordi; Laveille, Christian; Frederiksen, Rikke; Asnaghi, Veronica; Ballabio, Maria; Jacqmin, Philippe; de Min, Cristina.
Afiliação
  • De Benedetti F; Division of Rheumatology, Ospedale Pediatrico Bambino Gesù, IRCCS, Rome, Italy fabrizio.debenedetti@opbg.net.
  • Grom AA; Division of Rheumatology, Cincinnati Children's Hospital Medical Center, Cincinnati, OH, USA.
  • Brogan PA; Department of Pediatrics, University of Cincinnati College of Medicine, Cincinnati, OH, USA.
  • Bracaglia C; University College London Great Ormond Street Institute of Child Health, London, UK.
  • Pardeo M; Division of Rheumatology, Ospedale Pediatrico Bambino Gesù, IRCCS, Rome, Italy.
  • Marucci G; Division of Rheumatology, Ospedale Pediatrico Bambino Gesù, IRCCS, Rome, Italy.
  • Eleftheriou D; Division of Rheumatology, Ospedale Pediatrico Bambino Gesù, IRCCS, Rome, Italy.
  • Papadopoulou C; University College London Great Ormond Street Institute of Child Health, London, UK.
  • Schulert GS; University College London Great Ormond Street Institute of Child Health, London, UK.
  • Quartier P; Division of Rheumatology, Cincinnati Children's Hospital Medical Center, Cincinnati, OH, USA.
  • Antón J; Department of Pediatrics, University of Cincinnati College of Medicine, Cincinnati, OH, USA.
  • Laveille C; Pediatric Immuno-Hematology and Rheumatology Unit, RAISE Rare Disease Reference Centre, Hopital Universitaire Necker-Enfants Malades, Assistance Publique-Hopitaux de Paris, Paris, France.
  • Frederiksen R; Université Paris-Cité, Paris, France.
  • Asnaghi V; Pediatric Rheumatology, Hospital Sant Joan de Deu, Barcelona, Spain.
  • Ballabio M; Faculty of Medicine, Universitat de Barcelona, Barcelona, Spain.
  • Jacqmin P; Calvagone Sarl, Liergues, France.
  • de Min C; Swedish Orphan Biovitrum AG (Sobi), Basel, Switzerland.
Ann Rheum Dis ; 82(6): 857-865, 2023 06.
Article em En | MEDLINE | ID: mdl-37001971

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Artrite Juvenil / Doença de Still de Início Tardio / Síndrome de Ativação Macrofágica Tipo de estudo: Diagnostic_studies / Etiology_studies / Observational_studies / Prognostic_studies / Risk_factors_studies Limite: Adult / Humans Idioma: En Ano de publicação: 2023 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Artrite Juvenil / Doença de Still de Início Tardio / Síndrome de Ativação Macrofágica Tipo de estudo: Diagnostic_studies / Etiology_studies / Observational_studies / Prognostic_studies / Risk_factors_studies Limite: Adult / Humans Idioma: En Ano de publicação: 2023 Tipo de documento: Article