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GalNAc-Lipid nanoparticles enable non-LDLR dependent hepatic delivery of a CRISPR base editing therapy.
Kasiewicz, Lisa N; Biswas, Souvik; Beach, Aaron; Ren, Huilan; Dutta, Chaitali; Mazzola, Anne Marie; Rohde, Ellen; Chadwick, Alexandra; Cheng, Christopher; Garcia, Sara P; Iyer, Sowmya; Matsumoto, Yuri; Khera, Amit V; Musunuru, Kiran; Kathiresan, Sekar; Malyala, Padma; Rajeev, Kallanthottathil G; Bellinger, Andrew M.
Afiliação
  • Kasiewicz LN; Verve Therapeutics, 201 Brookline Avenue, Suite 601, Boston, MA, 02215, USA.
  • Biswas S; Verve Therapeutics, 201 Brookline Avenue, Suite 601, Boston, MA, 02215, USA.
  • Beach A; Verve Therapeutics, 201 Brookline Avenue, Suite 601, Boston, MA, 02215, USA.
  • Ren H; Verve Therapeutics, 201 Brookline Avenue, Suite 601, Boston, MA, 02215, USA.
  • Dutta C; Verve Therapeutics, 201 Brookline Avenue, Suite 601, Boston, MA, 02215, USA.
  • Mazzola AM; Verve Therapeutics, 201 Brookline Avenue, Suite 601, Boston, MA, 02215, USA.
  • Rohde E; Verve Therapeutics, 201 Brookline Avenue, Suite 601, Boston, MA, 02215, USA.
  • Chadwick A; Verve Therapeutics, 201 Brookline Avenue, Suite 601, Boston, MA, 02215, USA.
  • Cheng C; Verve Therapeutics, 201 Brookline Avenue, Suite 601, Boston, MA, 02215, USA.
  • Garcia SP; Verve Therapeutics, 201 Brookline Avenue, Suite 601, Boston, MA, 02215, USA.
  • Iyer S; Verve Therapeutics, 201 Brookline Avenue, Suite 601, Boston, MA, 02215, USA.
  • Matsumoto Y; Verve Therapeutics, 201 Brookline Avenue, Suite 601, Boston, MA, 02215, USA.
  • Khera AV; Verve Therapeutics, 201 Brookline Avenue, Suite 601, Boston, MA, 02215, USA.
  • Musunuru K; Division of Cardiovascular Medicine, Department of Medicine, Perelman School of Medicine at the University of Pennsylvania, Philadelphia, PA, USA.
  • Kathiresan S; Verve Therapeutics, 201 Brookline Avenue, Suite 601, Boston, MA, 02215, USA.
  • Malyala P; Verve Therapeutics, 201 Brookline Avenue, Suite 601, Boston, MA, 02215, USA.
  • Rajeev KG; Verve Therapeutics, 201 Brookline Avenue, Suite 601, Boston, MA, 02215, USA.
  • Bellinger AM; Verve Therapeutics, 201 Brookline Avenue, Suite 601, Boston, MA, 02215, USA. abellinger@vervetx.com.
Nat Commun ; 14(1): 2776, 2023 05 15.
Article em En | MEDLINE | ID: mdl-37188660

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Nanopartículas / Hipercolesterolemia Familiar Homozigota Limite: Animals Idioma: En Ano de publicação: 2023 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Nanopartículas / Hipercolesterolemia Familiar Homozigota Limite: Animals Idioma: En Ano de publicação: 2023 Tipo de documento: Article