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Correction to: Safety and effectiveness of ataluren in patients with nonsense mutation DMD in the STRIDE Registry compared with the CINRG Duchenne Natural History Study (2015-2022): 2022 interim analysis.
Mercuri, Eugenio; Osorio, Andrés Nascimento; Muntoni, Francesco; Buccella, Filippo; Desguerre, Isabelle; Kirschner, Janbernd; Tulinius, Már; de Resende, Maria Bernadete Dutra; Morgenroth, Lauren P; Gordish-Dressman, Heather; Johnson, Shelley; Kristensen, Allan; Werner, Christian; Trifillis, Panayiota; Henricson, Erik K; McDonald, Craig M.
Afiliação
  • Mercuri E; Department of Pediatric Neurology, Catholic University, Rome, Italy. eugeniomaria.mercuri@unicatt.it.
  • Osorio AN; Centro Clinico Nemo, Fondazione Policlinico Agostino Gemelli IRCCS, Rome, Italy. eugeniomaria.mercuri@unicatt.it.
  • Muntoni F; Neuromuscular Unit, Department of Neurology and Research in Neuromuscular Diseases, Institut de Recerca Sant Joan de Déu, Center for Biomedical Research Network on Rare Diseases (CIBERER), ISCIII, Barcelona, Spain.
  • Buccella F; UCL Great Ormond Street Institute of Child Health, London, UK.
  • Desguerre I; National Institute for Health Research, Great Ormond Street Institute of Child Health Biomedical Research Centre, University College London, London, UK.
  • Kirschner J; Parent Project APS, Rome, Italy.
  • Tulinius M; Hôpital Necker-Enfants Malades, Paris, France.
  • de Resende MBD; Department of Neuropediatrics and Muscle Disorders, Medical Center-University of Freiburg, Faculty of Medicine, Freiburg, Germany.
  • Morgenroth LP; Department of Pediatrics, Gothenburg University, Queen Silvia Children's Hospital, Gothenburg, Sweden.
  • Gordish-Dressman H; Department of Neurology, Faculty of Medicine, University of São Paulo, São Paulo, SP, Brazil.
  • Johnson S; Therapeutic Research in Neuromuscular Disorders Solutions (TRiNDS), Pittsburgh, PA, USA.
  • Kristensen A; Center for Genetic Medicine, Children's National Health System and the George Washington, Washington, DC, USA.
  • Werner C; PTC Therapeutics Inc., South Plainfield, NJ, USA.
  • Trifillis P; PTC Therapeutics Inc., South Plainfield, NJ, USA.
  • Henricson EK; PTC Therapeutics Germany GmbH, Frankfurt, Germany.
  • McDonald CM; PTC Therapeutics Inc., South Plainfield, NJ, USA.
J Neurol ; 270(9): 4583, 2023 Sep.
Article em En | MEDLINE | ID: mdl-37460854

Texto completo: 1 Base de dados: MEDLINE Idioma: En Ano de publicação: 2023 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Idioma: En Ano de publicação: 2023 Tipo de documento: Article