Prevention of early-onset cardiomyopathy in <i>Dmd</i> exon 52-54 deletion mice by CRISPR-Cas9-mediated exon skipping.

Rok, Matthew; Wong, Tatianna Wai Ying; Maino, Eleonora; Ahmed, Abdalla; Yang, Grace; Hyatt, Elzbieta; Lindsay, Kyle; Fatehi, Sina; Marks, Ryan; Delgado-Olguín, Paul; Ivakine, Evgueni A; Cohn, Ronald D

Prevention of early-onset cardiomyopathy in Dmd exon 52-54 deletion mice by CRISPR-Cas9-mediated exon skipping.

Rok, Matthew; Wong, Tatianna Wai Ying; Maino, Eleonora; Ahmed, Abdalla; Yang, Grace; Hyatt, Elzbieta; Lindsay, Kyle; Fatehi, Sina; Marks, Ryan; Delgado-Olguín, Paul; Ivakine, Evgueni A; Cohn, Ronald D.

Afiliação

Rok M; Program in Genetics and Genome Biology, The Hospital for Sick Children Research Institute, Toronto, ON, Canada.
Wong TWY; Department of Molecular Genetics, University of Toronto, Toronto, ON, Canada.
Maino E; Program in Genetics and Genome Biology, The Hospital for Sick Children Research Institute, Toronto, ON, Canada.
Ahmed A; Department of Molecular Genetics, University of Toronto, Toronto, ON, Canada.
Yang G; Program in Genetics and Genome Biology, The Hospital for Sick Children Research Institute, Toronto, ON, Canada.
Hyatt E; Department of Molecular Genetics, University of Toronto, Toronto, ON, Canada.
Lindsay K; Department of Translational Medicine, The Hospital for Sick Children, Toronto, ON, Canada.
Fatehi S; Department of Biochemistry & Biomedical Sciences, McMaster University, Hamilton, ON, Canada.
Marks R; Program in Genetics and Genome Biology, The Hospital for Sick Children Research Institute, Toronto, ON, Canada.
Delgado-Olguín P; Program in Genetics and Genome Biology, The Hospital for Sick Children Research Institute, Toronto, ON, Canada.
Ivakine EA; Program in Genetics and Genome Biology, The Hospital for Sick Children Research Institute, Toronto, ON, Canada.
Cohn RD; Department of Molecular Genetics, University of Toronto, Toronto, ON, Canada.