Real-life experience with a generic formulation of lumacaftor-ivacaftor in patients with cystic fibrosis homozygous for the Phe508del CFTR mutation.
Pediatr Pulmonol
; 58(12): 3560-3565, 2023 Dec.
Article
em En
| MEDLINE
| ID: mdl-37712606
Texto completo:
1
Base de dados:
MEDLINE
Assunto principal:
Fibrose Cística
Limite:
Adolescent
/
Child
/
Female
/
Humans
/
Male
Idioma:
En
Ano de publicação:
2023
Tipo de documento:
Article