Gene therapy-based strategies for spinal muscular atrophy-an Asia-Pacific perspective.

Farrar, Michelle A; Calotes-Castillo, Loudella; De Silva, Ranil; Barclay, Peter; Attwood, Lani; Cini, Julie; Ferrie, Monica; Kariyawasam, Didu S.

Afiliação

Farrar MA; Department of Neurology, Sydney Children's Hospital Network, Sydney, New South Wales, Australia. m.farrar@unsw.edu.au.
Calotes-Castillo L; Discipline of Paediatrics and Child Health, UNSW Medicine and Health, School of Clinical Medicine, UNSW Sydney, Sydney, New South Wales, Australia. m.farrar@unsw.edu.au.
De Silva R; Division of Paediatric Neurology, Department of Paediatrics and Neurosciences, University of the Philippines - Philippine General Hospital, Manila, Philippines.
Barclay P; Faculty of Medical Sciences, Interdisciplinary Centre for Innovation in Biotechnology and Neuroscience (ICIBN), University of Sri Jayewardenepura, Nugegoda, Sri Lanka.
Attwood L; Institute for Combinatorial Advanced Research and Education, General Sir John Kotelawala Defence University, Ratmalana, Sri Lanka.
Cini J; Pharmacy Department, Sydney Children's Hospitals Network, Sydney, New South Wales, Australia.
Ferrie M; Kids Advanced Therapeutics Programme, Sydney Children's Hospitals Network, Kids Research, Sydney, New South Wales, Australia.
Kariyawasam DS; Advocacy Beyond Borders, Melbourne, Australia.

Mol Cell Pediatr ; 10(1): 17, 2023 Nov 15.

Article em En | MEDLINE | ID: mdl-37964159