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Challenges and opportunities in neurometabolic disease treatment with enzyme delivery.
Begley, David; Gabathuler, Reinhard; Pastores, Gregory; Garcia-Cazorla, Angeles; Ardigò, Diego; Scarpa, Maurizio; Tomanin, Rosella; Tosi, Giovanni.
Afiliação
  • Begley D; Blood-Brain Barrier Group, King's College London, Strand, London, UK.
  • Gabathuler R; Blood-Brain Barrier Group, King's College London, Strand, London, UK.
  • Pastores G; Medicine, University College Dublin, Belfield, Dublin, Ireland.
  • Garcia-Cazorla A; Neurometabolic Unit. Department of Neurology, Hospital Sant Joan de Déu, CIBERER and MetabERN, Barcelona, Spain.
  • Ardigò D; Chiesi Farmaceutici S.p.A, Parma, Italy.
  • Scarpa M; Regional Coordinating Center for Rare Diseases, Udine University Hospital, Udine, Italy.
  • Tomanin R; Laboratory of Diagnosis and Therapy of Lysosomal Disorders, Dept. of Women's and Children's Health, University of Padova, Padova, Italy.
  • Tosi G; Istituto di Ricerca Pediatrica Città della Speranza, Padova, Italy.
Expert Opin Drug Deliv ; 21(6): 817-828, 2024 Jun.
Article em En | MEDLINE | ID: mdl-38963225

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Barreira Hematoencefálica / Sistemas de Liberação de Medicamentos Limite: Animals / Humans Idioma: En Ano de publicação: 2024 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Barreira Hematoencefálica / Sistemas de Liberação de Medicamentos Limite: Animals / Humans Idioma: En Ano de publicação: 2024 Tipo de documento: Article