Detalhe da pesquisa
1.
T-cell gene therapy for perforin deficiency corrects cytotoxicity defects and prevents hemophagocytic lymphohistiocytosis manifestations.
J Allergy Clin Immunol
; 142(3): 904-913.e3, 2018 09.
Artigo
em Inglês
| MEDLINE | ID: mdl-29355678
2.
Sheep CD34+ amniotic fluid cells have hematopoietic potential and engraft after autologous in utero transplantation.
Stem Cells
; 33(1): 122-32, 2015 Jan.
Artigo
em Inglês
| MEDLINE | ID: mdl-25186828
3.
Perforin gene transfer into hematopoietic stem cells improves immune dysregulation in murine models of perforin deficiency.
Mol Ther
; 23(4): 737-45, 2015 Apr.
Artigo
em Inglês
| MEDLINE | ID: mdl-25523759
4.
Megakaryocytes assemble podosomes that degrade matrix and protrude through basement membrane.
Blood
; 121(13): 2542-52, 2013 Mar 28.
Artigo
em Inglês
| MEDLINE | ID: mdl-23305739
5.
Preclinical demonstration of lentiviral vector-mediated correction of immunological and metabolic abnormalities in models of adenosine deaminase deficiency.
Mol Ther
; 22(3): 607-622, 2014 Mar.
Artigo
em Inglês
| MEDLINE | ID: mdl-24256635
6.
Unregulated actin polymerization by WASp causes defects of mitosis and cytokinesis in X-linked neutropenia.
J Exp Med
; 204(9): 2213-24, 2007 Sep 03.
Artigo
em Inglês
| MEDLINE | ID: mdl-17724125
7.
Functional human artificial chromosomes are generated and stably maintained in human embryonic stem cells.
Hum Mol Genet
; 20(15): 2905-13, 2011 Aug 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-21593218
8.
Cytoskeletal remodeling mediated by WASp in dendritic cells is necessary for normal immune synapse formation and T-cell priming.
Blood
; 118(9): 2492-501, 2011 Sep 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-21690559
9.
The ß-globin locus control region in combination with the EF1α short promoter allows enhanced lentiviral vector-mediated erythroid gene expression with conserved multilineage activity.
Mol Ther
; 20(7): 1400-9, 2012 Jul.
Artigo
em Inglês
| MEDLINE | ID: mdl-22434141
10.
Valproic acid confers functional pluripotency to human amniotic fluid stem cells in a transgene-free approach.
Mol Ther
; 20(10): 1953-67, 2012 Oct.
Artigo
em Inglês
| MEDLINE | ID: mdl-22760542
11.
Engraftment defect of cytokine-cultured adult human mobilized CD34(+) cells is related to reduced adhesion to bone marrow niche elements.
Br J Haematol
; 158(6): 778-87, 2012 Sep.
Artigo
em Inglês
| MEDLINE | ID: mdl-22816563
12.
Tyrosine phosphorylation of WASP promotes calpain-mediated podosome disassembly.
Haematologica
; 97(5): 687-91, 2012 May.
Artigo
em Inglês
| MEDLINE | ID: mdl-22133775
13.
Biochemical correction of X-CGD by a novel chimeric promoter regulating high levels of transgene expression in myeloid cells.
Mol Ther
; 19(1): 122-32, 2011 Jan.
Artigo
em Inglês
| MEDLINE | ID: mdl-20978475
14.
Phosphorylation of WASp is a key regulator of activity and stability in vivo.
Proc Natl Acad Sci U S A
; 106(37): 15738-43, 2009 Sep 15.
Artigo
em Inglês
| MEDLINE | ID: mdl-19805221
15.
Coordinated oncogenic transformation and inhibition of host immune responses by the PAX3-FKHR fusion oncoprotein.
J Exp Med
; 202(10): 1399-410, 2005 Nov 21.
Artigo
em Inglês
| MEDLINE | ID: mdl-16287709
16.
Lentivirus-mediated reprogramming of somatic cells in the absence of transgenic transcription factors.
Mol Ther
; 18(12): 2139-45, 2010 Dec.
Artigo
em Inglês
| MEDLINE | ID: mdl-20978477
17.
Flow Cytometry as an Important Tool in Proteomic Profiling.
Methods Mol Biol
; 2261: 213-227, 2021.
Artigo
em Inglês
| MEDLINE | ID: mdl-33420992
18.
Nonintegrating lentivector vaccines stimulate prolonged T-cell and antibody responses and are effective in tumor therapy.
J Virol
; 83(7): 3094-103, 2009 Apr.
Artigo
em Inglês
| MEDLINE | ID: mdl-19176629
19.
Improvement of migratory defects in a murine model of Wiskott-Aldrich syndrome gene therapy.
Mol Ther
; 16(5): 836-44, 2008 May.
Artigo
em Inglês
| MEDLINE | ID: mdl-18388921
20.
Publisher Correction: In Utero Gene Therapy (IUGT) Using GLOBE Lentiviral Vector Phenotypically Corrects the Heterozygous Humanised Mouse Model and Its Progress Can Be Monitored Using MRI Techniques.
Sci Rep
; 9(1): 20214, 2019 Dec 24.
Artigo
em Inglês
| MEDLINE | ID: mdl-31874968