Detalhe da pesquisa
1.
Nr2e3 is a genetic modifier that rescues retinal degeneration and promotes homeostasis in multiple models of retinitis pigmentosa.
Gene Ther
; 28(5): 223-241, 2021 05.
Artigo
em Inglês
| MEDLINE | ID: mdl-32123325
2.
Small Molecule-Based Inducible Gene Therapies for Retinal Degeneration.
Adv Exp Med Biol
; 1185: 65-69, 2019.
Artigo
em Inglês
| MEDLINE | ID: mdl-31884590
3.
Synonymous variants in HTRA1 implicated in AMD susceptibility impair its capacity to regulate TGF-ß signaling.
Hum Mol Genet
; 24(22): 6361-73, 2015 Nov 15.
Artigo
em Inglês
| MEDLINE | ID: mdl-26310622
4.
Utility of the DHFR-based destabilizing domain across mouse models of retinal degeneration and aging.
iScience
; 25(5): 104206, 2022 May 20.
Artigo
em Inglês
| MEDLINE | ID: mdl-35521529
5.
Fibulin-3 knockout mice demonstrate corneal dysfunction but maintain normal retinal integrity.
J Mol Med (Berl)
; 98(11): 1639-1656, 2020 11.
Artigo
em Inglês
| MEDLINE | ID: mdl-32964303
6.
Non-antibiotic Small-Molecule Regulation of DHFR-Based Destabilizing Domains In Vivo.
Mol Ther Methods Clin Dev
; 15: 27-39, 2019 Dec 13.
Artigo
em Inglês
| MEDLINE | ID: mdl-31649953
7.
A Destabilizing Domain Allows for Fast, Noninvasive, Conditional Control of Protein Abundance in the Mouse Eye - Implications for Ocular Gene Therapy.
Invest Ophthalmol Vis Sci
; 59(12): 4909-4920, 2018 10 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-30347085