Detalhe da pesquisa
1.
AAV2 vector optimization for retinal ganglion cell-targeted delivery of therapeutic genes.
Gene Ther
; 31(3-4): 175-186, 2024 Mar.
Artigo
em Inglês
| MEDLINE | ID: mdl-38200264
2.
Rescue of retinal ganglion cells in optic nerve injury using cell-selective AAV mediated delivery of SIRT1.
Gene Ther
; 28(5): 256-264, 2021 05.
Artigo
em Inglês
| MEDLINE | ID: mdl-33589779
3.
A Mini Review: Moving iPSC-Derived Retinal Subtypes Forward for Clinical Applications for Retinal Degenerative Diseases.
Adv Exp Med Biol
; 1185: 557-561, 2019.
Artigo
em Inglês
| MEDLINE | ID: mdl-31884670
4.
Cell-Specific Expression of Human SIRT1 by Gene Therapy Reduces Retinal Ganglion Cell Loss Induced by Elevated Intraocular Pressure.
Neurotherapeutics
; 20(3): 896-907, 2023 Apr.
Artigo
em Inglês
| MEDLINE | ID: mdl-36941497
5.
Selective Upregulation of SIRT1 Expression in Retinal Ganglion Cells by AAV-Mediated Gene Delivery Increases Neuronal Cell Survival and Alleviates Axon Demyelination Associated with Optic Neuritis.
Biomolecules
; 12(6)2022 06 14.
Artigo
em Inglês
| MEDLINE | ID: mdl-35740955
6.
Dual SMAD inhibition and Wnt inhibition enable efficient and reproducible differentiations of induced pluripotent stem cells into retinal ganglion cells.
Sci Rep
; 10(1): 11828, 2020 07 16.
Artigo
em Inglês
| MEDLINE | ID: mdl-32678240
7.
CRISPR Activation Enhances In Vitro Potency of AAV Vectors Driven by Tissue-Specific Promoters.
Mol Ther Methods Clin Dev
; 13: 380-389, 2019 Jun 14.
Artigo
em Inglês
| MEDLINE | ID: mdl-31024980
8.
Comparative AAV-eGFP Transgene Expression Using Vector Serotypes 1-9, 7m8, and 8b in Human Pluripotent Stem Cells, RPEs, and Human and Rat Cortical Neurons.
Stem Cells Int
; 2019: 7281912, 2019.
Artigo
em Inglês
| MEDLINE | ID: mdl-30800164
9.
Use of induced pluripotent stem cell models to probe the pathogenesis of Choroideremia and to develop a potential treatment.
Stem Cell Res
; 27: 140-150, 2018 03.
Artigo
em Inglês
| MEDLINE | ID: mdl-29414605
10.
Author Correction: An Autogenously Regulated Expression System for Gene Therapeutic Ocular Applications.
Sci Rep
; 8(1): 17286, 2018 Nov 23.
Artigo
em Inglês
| MEDLINE | ID: mdl-30470797
11.
Retinas in a Dish Peek into Inherited Retinal Degeneration.
Cell Stem Cell
; 18(6): 688-689, 2016 06 02.
Artigo
em Inglês
| MEDLINE | ID: mdl-27257755