Detalhe da pesquisa
1.
Impaired myogenic development, differentiation and function in hESC-derived SMA myoblasts and myotubes.
PLoS One
; 13(10): e0205589, 2018.
Artigo
em Inglês
| MEDLINE | ID: mdl-30304024
2.
Motor neuron disease. SMN2 splicing modifiers improve motor function and longevity in mice with spinal muscular atrophy.
Science
; 345(6197): 688-93, 2014 Aug 08.
Artigo
em Inglês
| MEDLINE | ID: mdl-25104390