Detalhe da pesquisa
1.
High-dose systemic adeno-associated virus vector administration causes liver and sinusoidal endothelial cell injury.
Mol Ther
; 32(4): 952-968, 2024 Apr 03.
Artigo
em Inglês
| MEDLINE | ID: mdl-38327046
2.
The GPI-Linked Protein LY6A Drives AAV-PHP.B Transport across the Blood-Brain Barrier.
Mol Ther
; 27(5): 912-921, 2019 05 08.
Artigo
em Inglês
| MEDLINE | ID: mdl-30819613
3.
Inactivation of the interleukin-22 pathway in the airways of cystic fibrosis patients.
Cytokine
; 113: 470-474, 2019 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-30377053
4.
The Neurotropic Properties of AAV-PHP.B Are Limited to C57BL/6J Mice.
Mol Ther
; 26(3): 664-668, 2018 03 07.
Artigo
em Inglês
| MEDLINE | ID: mdl-29428298
5.
Quantification of human mature frataxin protein expression in nonhuman primate hearts after gene therapy.
Res Sq
; 2023 Jun 29.
Artigo
em Inglês
| MEDLINE | ID: mdl-37461697
6.
Quantification of human mature frataxin protein expression in nonhuman primate hearts after gene therapy.
Commun Biol
; 6(1): 1093, 2023 10 27.
Artigo
em Inglês
| MEDLINE | ID: mdl-37891254
7.
Immune transgene-dependent myocarditis in macaques after systemic administration of adeno-associated virus expressing human acid alpha-glucosidase.
Front Immunol
; 14: 1094279, 2023.
Artigo
em Inglês
| MEDLINE | ID: mdl-37033976
8.
Positron Emission Tomography Quantitative Assessment of Off-Target Whole-Body Biodistribution of I-124-Labeled Adeno-Associated Virus Capsids Administered to Cerebral Spinal Fluid.
Hum Gene Ther
; 34(21-22): 1095-1106, 2023 Nov.
Artigo
em Inglês
| MEDLINE | ID: mdl-37624734
9.
Efficacy and Safety of a Krabbe Disease Gene Therapy.
Hum Gene Ther
; 33(9-10): 499-517, 2022 05.
Artigo
em Inglês
| MEDLINE | ID: mdl-35333110
10.
MicroRNA-mediated inhibition of transgene expression reduces dorsal root ganglion toxicity by AAV vectors in primates.
Sci Transl Med
; 12(569)2020 11 11.
Artigo
em Inglês
| MEDLINE | ID: mdl-33177182
11.
Adeno-Associated Virus-Induced Dorsal Root Ganglion Pathology.
Hum Gene Ther
; 31(15-16): 808-818, 2020 08.
Artigo
em Inglês
| MEDLINE | ID: mdl-32845779
12.
Randomized, double-blind trial of F14512, a polyamine-vectorized anticancer drug, compared with etoposide phosphate, in dogs with naturally occurring lymphoma.
Oncotarget
; 11(7): 671-686, 2020 Feb 18.
Artigo
em Inglês
| MEDLINE | ID: mdl-32133044
13.
Intra-CSF AAV9 and AAVrh10 Administration in Nonhuman Primates: Promising Routes and Vectors for Which Neurological Diseases?
Mol Ther Methods Clin Dev
; 17: 771-784, 2020 Jun 12.
Artigo
em Inglês
| MEDLINE | ID: mdl-32355866
14.
Safe and Sustained Expression of Human Iduronidase After Intrathecal Administration of Adeno-Associated Virus Serotype 9 in Infant Rhesus Monkeys.
Hum Gene Ther
; 30(8): 957-966, 2019 08.
Artigo
em Inglês
| MEDLINE | ID: mdl-31017018
15.
Standardized Method for Intra-Cisterna Magna Delivery Under Fluoroscopic Guidance in Nonhuman Primates.
Hum Gene Ther Methods
; 29(5): 212-219, 2018 10.
Artigo
em Inglês
| MEDLINE | ID: mdl-30032644
16.
Toxicology Study of Intra-Cisterna Magna Adeno-Associated Virus 9 Expressing Iduronate-2-Sulfatase in Rhesus Macaques.
Mol Ther Methods Clin Dev
; 10: 68-78, 2018 Sep 21.
Artigo
em Inglês
| MEDLINE | ID: mdl-30073178
17.
Toxicology Study of Intra-Cisterna Magna Adeno-Associated Virus 9 Expressing Human Alpha-L-Iduronidase in Rhesus Macaques.
Mol Ther Methods Clin Dev
; 10: 79-88, 2018 Sep 21.
Artigo
em Inglês
| MEDLINE | ID: mdl-30073179
18.
Dose escalation study to evaluate safety, tolerability and efficacy of intravenous etoposide phosphate administration in 27 dogs with multicentric lymphoma.
PLoS One
; 12(5): e0177486, 2017.
Artigo
em Inglês
| MEDLINE | ID: mdl-28505195