Detalhe da pesquisa
1.
Efanesoctocog Alfa Prophylaxis for Patients with Severe Hemophilia A.
N Engl J Med
; 388(4): 310-318, 2023 01 26.
Artigo
em Inglês
| MEDLINE | ID: mdl-36720133
2.
Gene Therapy with Etranacogene Dezaparvovec for Hemophilia B.
N Engl J Med
; 388(8): 706-718, 2023 02 23.
Artigo
em Inglês
| MEDLINE | ID: mdl-36812434
3.
Benefits and risks of non-factor therapies: Redefining haemophilia treatment goals in the era of new technologies.
Haemophilia
; 30 Suppl 3: 39-44, 2024 Apr.
Artigo
em Inglês
| MEDLINE | ID: mdl-38481077
4.
Measurement of recombinant porcine factor VIII in patients with congenital haemophilia A and inhibitors in the presence of emicizumab.
Haemophilia
; 30(2): 545-553, 2024 Mar.
Artigo
em Inglês
| MEDLINE | ID: mdl-38343119
5.
Indirect treatment comparisons of the gene therapy etranacogene dezaparvovec versus extended half-life factor IX therapies for severe or moderately severe haemophilia B.
Haemophilia
; 30(1): 75-86, 2024 Jan.
Artigo
em Inglês
| MEDLINE | ID: mdl-37902714
6.
Rurioctocog alfa pegol PK-guided prophylaxis in hemophilia A: results from the phase 3 PROPEL study.
Blood
; 137(13): 1818-1827, 2021 04 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-33150384
7.
Synovitis and joint health in patients with haemophilia: Statements from a European e-Delphi consensus study.
Haemophilia
; 29(2): 619-628, 2023 Mar.
Artigo
em Inglês
| MEDLINE | ID: mdl-36622258
8.
Real-world evidence on efmoroctocog alfa in patients with haemophilia A: A systematic literature review of treatment experience in Europe.
Haemophilia
; 29(4): 963-974, 2023 Jul.
Artigo
em Inglês
| MEDLINE | ID: mdl-37243934
9.
Matching-adjusted indirect comparison of bleeding outcomes in severe haemophilia A: Comparing valoctocogene roxaparvovec gene therapy, emicizumab prophylaxis, and FVIII replacement prophylaxis.
Haemophilia
; 29(4): 1087-1094, 2023 Jul.
Artigo
em Inglês
| MEDLINE | ID: mdl-37347645
10.
Accreditation model of European Haemophilia Centres in the era of novel treatments and gene therapy.
Haemophilia
; 29(6): 1442-1449, 2023 Nov.
Artigo
em Inglês
| MEDLINE | ID: mdl-37819168
11.
Applicability of the European Society of Cardiology Guidelines on the management of acute coronary syndromes to older people with haemophilia A - A modified Delphi consensus by the ADVANCE Working Group.
Haemophilia
; 29(1): 21-32, 2023 Jan.
Artigo
em Inglês
| MEDLINE | ID: mdl-36271497
12.
Bleeding and response to hemostatic therapy in acquired hemophilia A: results from the GTH-AH 01/2010 study.
Blood
; 136(3): 279-287, 2020 07 16.
Artigo
em Inglês
| MEDLINE | ID: mdl-32268359
13.
Immune tolerance induction in the era of emicizumab - still the first choice for patients with haemophilia A and inhibitors?
Haemophilia
; 28(2): 215-222, 2022 Mar.
Artigo
em Inglês
| MEDLINE | ID: mdl-34918839
14.
Electronic diaries in the management of haemophilia gene therapy: Perspective of an expert group from the German, Austrian and Swiss Society on Thrombosis and Haemostasis (GTH).
Haemophilia
; 28(2): 264-269, 2022 Mar.
Artigo
em Inglês
| MEDLINE | ID: mdl-35182445
15.
Factor VIII activity and bleeding risk during prophylaxis for severe hemophilia A: a population pharmacokinetic model.
Haematologica
; 106(7): 1902-1909, 2021 07 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-32327501
16.
Redefining prophylaxis in the modern era.
Haemophilia
; 27 Suppl 3: 21-27, 2021 Feb.
Artigo
em Inglês
| MEDLINE | ID: mdl-32469108
17.
Optimizing the management of patients with haemophilia A and inhibitors in the era of emicizumab: Recommendations from a German expert panel.
Haemophilia
; 27(3): e305-e313, 2021 May.
Artigo
em Inglês
| MEDLINE | ID: mdl-32937002
18.
Delivery of AAV-based gene therapy through haemophilia centres-A need for re-evaluation of infrastructure and comprehensive care: A Joint publication of EAHAD and EHC.
Haemophilia
; 27(6): 967-973, 2021 Nov.
Artigo
em Inglês
| MEDLINE | ID: mdl-34553460
19.
Gene therapy with adeno-associated virus vector 5-human factor IX in adults with hemophilia B.
Blood
; 131(9): 1022-1031, 2018 03 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-29246900
20.
Barriers and challenges for the fast treatment of bleeds in the non-haemophilia treatment centre hospital setting.
Haemophilia
; 26(3): 422-430, 2020 May.
Artigo
em Inglês
| MEDLINE | ID: mdl-32147924