Detalhe da pesquisa
1.
Increasing the Specificity of AAV-Based Gene Editing through Self-Targeting and Short-Promoter Strategies.
Mol Ther
; 29(3): 1047-1056, 2021 03 03.
Artigo
em Inglês
| MEDLINE | ID: mdl-33359790
2.
CRISPR/Cas9-mediated in vivo gene targeting corrects hemostasis in newborn and adult factor IX-knockout mice.
Blood
; 133(26): 2745-2752, 2019 06 27.
Artigo
em Inglês
| MEDLINE | ID: mdl-30975639
3.
Prevalent and Disseminated Recombinant and Wild-Type Adeno-Associated Virus Integration in Macaques and Humans.
Hum Gene Ther
; 34(21-22): 1081-1094, 2023 Nov.
Artigo
em Inglês
| MEDLINE | ID: mdl-37930949
4.
A mutation-independent CRISPR-Cas9-mediated gene targeting approach to treat a murine model of ornithine transcarbamylase deficiency.
Sci Adv
; 6(7): eaax5701, 2020 02.
Artigo
em Inglês
| MEDLINE | ID: mdl-32095520
5.
Accurate and Rapid Sequence Analysis of Adeno-Associated Virus Plasmids by Illumina Next-Generation Sequencing.
Hum Gene Ther Methods
; 29(5): 201-211, 2018 10.
Artigo
em Inglês
| MEDLINE | ID: mdl-30051733