Detalhe da pesquisa
1.
Phase 3 Trial of Concizumab in Hemophilia with Inhibitors.
N Engl J Med
; 389(9): 783-794, 2023 Aug 31.
Artigo
em Inglês
| MEDLINE | ID: mdl-37646676
2.
A new population pharmacokinetic model for recombinant factor IX-Fc fusion concentrate including young children with haemophilia B.
Br J Clin Pharmacol
; 90(1): 220-231, 2024 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-37567779
3.
Long-term immunogenicity, efficacy and tolerability of simoctocog alfa in patients with severe haemophilia A who had completed the NuProtect study in previously untreated patients.
Haemophilia
; 29(4): 1005-1012, 2023 Jul.
Artigo
em Inglês
| MEDLINE | ID: mdl-37335546
4.
Emicizumab prophylaxis in haemophilia A with inhibitors: Three years follow-up from the UK Haemophilia Centre Doctors' Organisation (UKHCDO).
Haemophilia
; 29(3): 743-752, 2023 May.
Artigo
em Inglês
| MEDLINE | ID: mdl-36811304
5.
Simoctocog alfa (Nuwiq®) in previously untreated patients with severe haemophilia A-Final efficacy and safety results from the NuProtect study.
Eur J Haematol
; 111(4): 544-552, 2023 Oct.
Artigo
em Inglês
| MEDLINE | ID: mdl-37439123
6.
A review of the pharmacokinetics, efficacy and safety of high-purity factor X for the prophylactic treatment of hereditary factor X deficiency.
Haemophilia
; 28(4): 523-531, 2022 Jul.
Artigo
em Inglês
| MEDLINE | ID: mdl-35499465
7.
Immune tolerance induction in severe haemophilia A: A UKHCDO inhibitor and paediatric working party consensus update.
Haemophilia
; 27(6): 932-937, 2021 Nov.
Artigo
em Inglês
| MEDLINE | ID: mdl-34403546
8.
A gain-of-function variant in DIAPH1 causes dominant macrothrombocytopenia and hearing loss.
Blood
; 127(23): 2903-14, 2016 06 09.
Artigo
em Inglês
| MEDLINE | ID: mdl-26912466
9.
A high-throughput sequencing test for diagnosing inherited bleeding, thrombotic, and platelet disorders.
Blood
; 127(23): 2791-803, 2016 06 09.
Artigo
em Inglês
| MEDLINE | ID: mdl-27084890
10.
Factor XIII levels correlate with fibrinogen concentrations in patients with venous malformations.
Haemophilia
; 28(6): e251-e253, 2022 11.
Artigo
em Inglês
| MEDLINE | ID: mdl-36084282
11.
An 11-year experience of acquired von Willebrand syndrome in children diagnosed with Wilms tumour in a tertiary referral centre.
Pediatr Blood Cancer
; 64(3)2017 03.
Artigo
em Inglês
| MEDLINE | ID: mdl-27616321
12.
Subcutaneous protein C concentrate in the management of severe protein C deficiency--experience from 12 centres.
Br J Haematol
; 164(3): 414-21, 2014 Feb.
Artigo
em Inglês
| MEDLINE | ID: mdl-24422725
13.
Design of a Real-World Observational Study in Previously Untreated and Minimally Treated Hemophilia A Patients: Protect-NOW.
TH Open
; 7(2): e110-e116, 2023 Apr.
Artigo
em Inglês
| MEDLINE | ID: mdl-37180427
14.
Unusual giant calculus of the submandibular duct: Case report and literature review.
Int J Surg Case Rep
; 84: 106139, 2021 Jul.
Artigo
em Inglês
| MEDLINE | ID: mdl-34216915
15.
A Novel, Enriched Population Pharmacokinetic Model for Recombinant Factor VIII-Fc Fusion Protein Concentrate in Hemophilia A Patients.
Thromb Haemost
; 120(5): 747-757, 2020 May.
Artigo
em Inglês
| MEDLINE | ID: mdl-32369846
16.
Guideline for the diagnosis and management of the rare coagulation disorders: a United Kingdom Haemophilia Centre Doctors' Organization guideline on behalf of the British Committee for Standards in Haematology.
Br J Haematol
; 167(3): 304-26, 2014 Nov.
Artigo
em Inglês
| MEDLINE | ID: mdl-25100430
17.
Prophylaxis in severe prothrombin deficiency.
Br J Haematol
; 152(2): 243-4, 2011 Jan.
Artigo
em Inglês
| MEDLINE | ID: mdl-20950404
18.
Therapeutic and routine prophylactic properties of rFactor VIII Fc (efraloctocog alfa, Eloctate®) in hemophilia A.
J Blood Med
; 7: 187-198, 2016.
Artigo
em Inglês
| MEDLINE | ID: mdl-27695377
19.
Venous thromboembolism occurring during adolescence.
Arch Dis Child
; 101(5): 427-32, 2016 May.
Artigo
em Inglês
| MEDLINE | ID: mdl-26787610
20.
A dominant gain-of-function mutation in universal tyrosine kinase SRC causes thrombocytopenia, myelofibrosis, bleeding, and bone pathologies.
Sci Transl Med
; 8(328): 328ra30, 2016 Mar 02.
Artigo
em Inglês
| MEDLINE | ID: mdl-26936507