Detalhe da pesquisa
1.
ZFN-Mediated In Vivo Genome Editing Corrects Murine Hurler Syndrome.
Mol Ther
; 27(1): 178-187, 2019 01 02.
Artigo
em Inglês
| MEDLINE | ID: mdl-30528089
2.
Dose-Dependent Prevention of Metabolic and Neurologic Disease in Murine MPS II by ZFN-Mediated In Vivo Genome Editing.
Mol Ther
; 26(4): 1127-1136, 2018 04 04.
Artigo
em Inglês
| MEDLINE | ID: mdl-29580682
3.
Robust ZFN-mediated genome editing in adult hemophilic mice.
Blood
; 122(19): 3283-7, 2013 Nov 07.
Artigo
em Inglês
| MEDLINE | ID: mdl-24085764
4.
A sensitive AAV transduction inhibition assay assists evaluation of critical factors for detection and concordance of pre-existing antibodies.
Mol Ther Methods Clin Dev
; 31: 101126, 2023 Dec 14.
Artigo
em Inglês
| MEDLINE | ID: mdl-37920239