Detalhe da pesquisa
1.
APOE ε4 and late-life cognition: mediation by structural brain imaging markers.
Eur J Epidemiol
; 37(6): 591-601, 2022 Jun.
Artigo
em Inglês
| MEDLINE | ID: mdl-35471691
2.
Deflazacort vs prednisone treatment for Duchenne muscular dystrophy: A meta-analysis of disease progression rates in recent multicenter clinical trials.
Muscle Nerve
; 61(1): 26-35, 2020 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-31599456
3.
Genotype and Lifetime Burden of Disease in Hypertrophic Cardiomyopathy: Insights from the Sarcomeric Human Cardiomyopathy Registry (SHaRe).
Circulation
; 138(14): 1387-1398, 2018 10 02.
Artigo
em Inglês
| MEDLINE | ID: mdl-30297972
4.
Real-World Outcomes of Acute Ischemic Stroke Treatment with Intravenous Recombinant Tissue Plasminogen Activator.
J Stroke Cerebrovasc Dis
; 26(9): 1996-2003, 2017 Sep.
Artigo
em Inglês
| MEDLINE | ID: mdl-28689999
5.
Late-life Cognitive Activity and Dementia: A Systematic Review and Bias Analysis.
Epidemiology
; 27(5): 732-42, 2016 09.
Artigo
em Inglês
| MEDLINE | ID: mdl-27227783
6.
Stratified Patient Profiling for Vedolizumab Effectiveness in Crohn's Disease: Identifying Optimal Subgroups for Enhanced Treatment Response in the EVOLVE Study.
Adv Ther
; 41(6): 2324-2341, 2024 Jun.
Artigo
em Inglês
| MEDLINE | ID: mdl-38658485
7.
Long-Term Comparative Efficacy and Safety of Risdiplam and Nusinersen in Children with Type 1 Spinal Muscular Atrophy.
Adv Ther
; 41(6): 2414-2434, 2024 Jun.
Artigo
em Inglês
| MEDLINE | ID: mdl-38705943
8.
Functional trajectories before and after loss of ambulation in Duchenne muscular dystrophy and implications for clinical trials.
PLoS One
; 19(6): e0304099, 2024.
Artigo
em Inglês
| MEDLINE | ID: mdl-38829874
9.
Analysis of 34 candidate genes in bupropion and placebo remission.
Int J Neuropsychopharmacol
; 16(4): 771-81, 2013 May.
Artigo
em Inglês
| MEDLINE | ID: mdl-22947179
10.
Longitudinal Assessment of Creatine Kinase, Creatine/Creatinineratio, and Myostatin as Monitoring Biomarkers in Becker Muscular Dystrophy.
Neurology
; 100(9): e975-e984, 2023 02 28.
Artigo
em Inglês
| MEDLINE | ID: mdl-36849458
11.
DMD Genotypes and Motor Function in Duchenne Muscular Dystrophy: A Multi-institution Meta-analysis With Implications for Clinical Trials.
Neurology
; 100(15): e1540-e1554, 2023 04 11.
Artigo
em Inglês
| MEDLINE | ID: mdl-36725339
12.
Health-Related Quality of Life Following Allogeneic Hematopoietic Cell Transplantation with Omidubicel versus Umbilical Cord Blood.
Transplant Cell Ther
; 29(1): 52.e1-52.e9, 2023 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-36179986
13.
Real-world and natural history data for drug evaluation in Duchenne muscular dystrophy: suitability of the North Star Ambulatory Assessment for comparisons with external controls.
Neuromuscul Disord
; 32(4): 271-283, 2022 04.
Artigo
em Inglês
| MEDLINE | ID: mdl-35396092
14.
Indirect treatment comparison of the efficacy of patisiran and inotersen for hereditary transthyretin-mediated amyloidosis with polyneuropathy.
Expert Opin Pharmacother
; 22(1): 121-129, 2021 Jan.
Artigo
em Inglês
| MEDLINE | ID: mdl-32892660
15.
Primary Hyperoxaluria Type 1 Disease Manifestations and Healthcare Utilization: A Multi-Country, Online, Chart Review Study.
Front Med (Lausanne)
; 8: 703305, 2021.
Artigo
em Inglês
| MEDLINE | ID: mdl-34616753
16.
Incidence of Parkinson's disease among hospital patients with methamphetamine-use disorders.
Mov Disord
; 25(14): 2333-9, 2010 Oct 30.
Artigo
em Inglês
| MEDLINE | ID: mdl-20737543
17.
Prognostic factors for changes in the timed 4-stair climb in patients with Duchenne muscular dystrophy, and implications for measuring drug efficacy: A multi-institutional collaboration.
PLoS One
; 15(6): e0232870, 2020.
Artigo
em Inglês
| MEDLINE | ID: mdl-32555695
18.
Suitability of external controls for drug evaluation in Duchenne muscular dystrophy.
Neurology
; 95(10): e1381-e1391, 2020 09 08.
Artigo
em Inglês
| MEDLINE | ID: mdl-32611643
19.
Categorising trajectories and individual item changes of the North Star Ambulatory Assessment in patients with Duchenne muscular dystrophy.
PLoS One
; 14(9): e0221097, 2019.
Artigo
em Inglês
| MEDLINE | ID: mdl-31479456
20.
Assessing Patient Preferences for Treatment Decisions for New Direct Acting Antiviral (DAA) Therapies for Chronic Hepatitis C Virus Infections.
Adv Ther
; 36(9): 2475-2486, 2019 09.
Artigo
em Inglês
| MEDLINE | ID: mdl-31240629