Detalhe da pesquisa
1.
A human genome editing-based MLL::AF4 ALL model recapitulates key cellular and molecular leukemogenic features.
Blood
; 142(20): 1752-1756, 2023 Nov 16.
Artigo
em Inglês
| MEDLINE | ID: mdl-37756522
2.
CRISPR/sgRNA-directed synergistic activation mediator (SAM) as a therapeutic tool for Parkinson´s disease.
Gene Ther
; 31(1-2): 31-44, 2024 Jan.
Artigo
em Inglês
| MEDLINE | ID: mdl-37542151
3.
Soluble mutant huntingtin drives early human pathogenesis in Huntington's disease.
Cell Mol Life Sci
; 80(8): 238, 2023 Aug 03.
Artigo
em Inglês
| MEDLINE | ID: mdl-37535170
4.
Lack of EGFR catalytic activity in hepatocytes improves liver regeneration following DDC-induced cholestatic injury by promoting a pro-restorative inflammatory response.
J Pathol
; 258(3): 312-324, 2022 11.
Artigo
em Inglês
| MEDLINE | ID: mdl-36148647
5.
Development and Characterization of a Factor V-Deficient CRISPR Cell Model for the Correction of Mutations.
Int J Mol Sci
; 23(10)2022 May 22.
Artigo
em Inglês
| MEDLINE | ID: mdl-35628611
6.
Natural estrogens enhance the engraftment of human hematopoietic stem and progenitor cells in immunodeficient mice.
Haematologica
; 106(6): 1659-1670, 2021 06 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-32354868
7.
The systemic administration of neural stem cells expressing an inducible and soluble form of growth arrest specific 1 inhibits mammary gland tumor growth and the formation of metastases.
Cytotherapy
; 23(3): 223-235, 2021 03.
Artigo
em Inglês
| MEDLINE | ID: mdl-33168454
8.
Targeted gene therapy into a safe harbor site in human hematopoietic progenitor cells.
Gene Ther
; 27(9): 435-450, 2020 09.
Artigo
em Inglês
| MEDLINE | ID: mdl-32218505
9.
Mitapivat versus Placebo for Pyruvate Kinase Deficiency.
N Engl J Med
; 386(26): 2538-2539, 2022 06 30.
Artigo
em Inglês
| MEDLINE | ID: mdl-35767453
10.
Advances in the gene therapy of monogenic blood cell diseases.
Clin Genet
; 97(1): 89-102, 2020 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-31231794
11.
c-Met Signaling Is Essential for Mouse Adult Liver Progenitor Cells Expansion After Transforming Growth Factor-ß-Induced Epithelial-Mesenchymal Transition and Regulates Cell Phenotypic Switch.
Stem Cells
; 37(8): 1108-1118, 2019 08.
Artigo
em Inglês
| MEDLINE | ID: mdl-31108004
12.
Curcumin downregulates Smad pathways and reduces hepatic stellate cells activation in experimental fibrosis.
Ann Hepatol
; 19(5): 497-506, 2020.
Artigo
em Inglês
| MEDLINE | ID: mdl-32673649
13.
ResUHUrge: A Low Cost and Fully Functional Ventilator Indicated for Application in COVID-19 Patients.
Sensors (Basel)
; 20(23)2020 Nov 27.
Artigo
em Inglês
| MEDLINE | ID: mdl-33260852
14.
Engraftment and in vivo proliferation advantage of gene-corrected mobilized CD34+ cells from Fanconi anemia patients.
Blood
; 130(13): 1535-1542, 2017 09 28.
Artigo
em Inglês
| MEDLINE | ID: mdl-28801449
15.
Addressing the diagnostic gaps in pyruvate kinase deficiency: Consensus recommendations on the diagnosis of pyruvate kinase deficiency.
Am J Hematol
; 94(1): 149-161, 2019 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-30358897
16.
Additive effects of the combined expression of soluble forms of GAS1 and PTEN inhibiting glioblastoma growth.
Gene Ther
; 25(6): 439-449, 2018 09.
Artigo
em Inglês
| MEDLINE | ID: mdl-29941984
17.
Annexin A1, Annexin A2, and Dyrk 1B are upregulated during GAS1-induced cell cycle arrest.
J Cell Physiol
; 233(5): 4166-4182, 2018 05.
Artigo
em Inglês
| MEDLINE | ID: mdl-29030970
18.
Comprehensive characterization of a novel, oncogenic and targetable SEPTIN6::ABL2 fusion in T-ALL.
Br J Haematol
; 202(3): 693-698, 2023 08.
Artigo
em Inglês
| MEDLINE | ID: mdl-37264982
19.
Mutations in the RACGAP1 gene cause autosomal recessive congenital dyserythropoietic anemia type III.
Haematologica
; 108(2): 581-587, 2023 02 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-36200420
20.
Expression of Gas1 in Mouse Brain: Release and Role in Neuronal Differentiation.
Cell Mol Neurobiol
; 38(4): 841-859, 2018 May.
Artigo
em Inglês
| MEDLINE | ID: mdl-29110208