1.
COPD
; 12 Suppl 1: 10-4, 2015 May.
Artigo
em Inglês
| MEDLINE
| ID: mdl-25938285
RESUMO
A Belgian alpha-1-antitrypsin (AAT) deficiency registry has been established in 2003. Currently 55 patients are included. At the same time, a working group has been set up for publishing national guidelines. In 2014, several Belgian patients founded Alpha-1 Global. We hope that the integrated activities of all the stakeholders involved in AAT deficiency will permit a high quality care for all patients suffering from this disabling disease.
Assuntos
Sistema de Registros , Deficiência de alfa 1-Antitripsina , Bélgica/epidemiologia , Feminino , Humanos , Cirrose Hepática/etiologia , Cirrose Hepática/cirurgia , Transplante de Fígado , Transplante de Pulmão , Masculino , Prevalência , Doença Pulmonar Obstrutiva Crônica/etiologia , Doença Pulmonar Obstrutiva Crônica/terapia , Enfisema Pulmonar/etiologia , Enfisema Pulmonar/terapia , Inibidores da Tripsina/uso terapêutico , alfa 1-Antitripsina/uso terapêutico , Deficiência de alfa 1-Antitripsina/complicações , Deficiência de alfa 1-Antitripsina/diagnóstico , Deficiência de alfa 1-Antitripsina/epidemiologia , Deficiência de alfa 1-Antitripsina/terapia
2.
Breathe (Sheff)
; 17(1): 200340, 2021 Mar.
Artigo
em Inglês
| MEDLINE
| ID: mdl-34295404
RESUMO
Three people with alpha-1 antitrypsin deficiency (AATD) share their experiences of living with this rare, genetic condition. They reflect on living with AATD and its impact on their lives including inequality of access to treatment across Europe. https://bit.ly/3rrYS9s.