Detalhe da pesquisa
1.
Recombinant ADAMTS13 in Congenital Thrombotic Thrombocytopenic Purpura.
N Engl J Med
; 390(17): 1584-1596, 2024 May 02.
Artigo
em Inglês
| MEDLINE | ID: mdl-38692292
2.
Phase 3 Trial of Concizumab in Hemophilia with Inhibitors.
N Engl J Med
; 389(9): 783-794, 2023 Aug 31.
Artigo
em Inglês
| MEDLINE | ID: mdl-37646676
3.
In Search of the Perfect Thrombosis and Bleeding-Associated Cancer Scale.
Semin Thromb Hemost
; 50(3): 443-454, 2024 Apr.
Artigo
em Inglês
| MEDLINE | ID: mdl-37852295
4.
Recombinant porcine factor VIII in patients with congenital haemophilia A with inhibitors undergoing surgery: Phase 3, single-arm, open-label study.
Haemophilia
; 30(2): 395-403, 2024 Mar.
Artigo
em Inglês
| MEDLINE | ID: mdl-38317504
5.
Phase 3 Trial of RNAi Therapeutic Givosiran for Acute Intermittent Porphyria.
N Engl J Med
; 382(24): 2289-2301, 2020 06 11.
Artigo
em Inglês
| MEDLINE | ID: mdl-32521132
6.
Rurioctocog alfa pegol PK-guided prophylaxis in hemophilia A: results from the phase 3 PROPEL study.
Blood
; 137(13): 1818-1827, 2021 04 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-33150384
7.
Annual incidence and severity of acute episodes in hereditary thrombotic thrombocytopenic purpura.
Blood
; 137(25): 3563-3575, 2021 06 24.
Artigo
em Inglês
| MEDLINE | ID: mdl-33649760
8.
Applicability of the European Society of Cardiology Guidelines on the management of acute coronary syndromes to older people with haemophilia A - A modified Delphi consensus by the ADVANCE Working Group.
Haemophilia
; 29(1): 21-32, 2023 Jan.
Artigo
em Inglês
| MEDLINE | ID: mdl-36271497
9.
Persistent imbalance, anti-apoptotic, and anti-inflammatory signature of circulating C-C chemokines and cytokines in patients with paroxysmal nocturnal hemoglobinuria.
Cytokine
; 150: 155780, 2022 02.
Artigo
em Inglês
| MEDLINE | ID: mdl-34896730
10.
Eptacog beta efficacy and safety in the treatment and control of bleeding in paediatric subjects (<12 years) with haemophilia A or B with inhibitors.
Haemophilia
; 28(4): 548-556, 2022 Jul.
Artigo
em Inglês
| MEDLINE | ID: mdl-35475308
11.
EXPLORE: A Prospective, Multinational, Natural History Study of Patients with Acute Hepatic Porphyria with Recurrent Attacks.
Hepatology
; 71(5): 1546-1558, 2020 05.
Artigo
em Inglês
| MEDLINE | ID: mdl-31512765
12.
Results of a randomized phase III/IV trial comparing intermittent bolus versus continuous infusion of antihaemophilic factor (recombinant) in adults with severe or moderately severe haemophilia A undergoing major orthopaedic surgery.
Haemophilia
; 27(3): e331-e339, 2021 May.
Artigo
em Inglês
| MEDLINE | ID: mdl-33772963
13.
PERSEPT 3: A phase 3 clinical trial to evaluate the haemostatic efficacy of eptacog beta (recombinant human FVIIa) in perioperative care in subjects with haemophilia A or B with inhibitors.
Haemophilia
; 27(6): 911-920, 2021 Nov.
Artigo
em Inglês
| MEDLINE | ID: mdl-34614267
14.
Emicizumab Prophylaxis in Hemophilia A with Inhibitors.
N Engl J Med
; 377(9): 809-818, 2017 08 31.
Artigo
em Inglês
| MEDLINE | ID: mdl-28691557
15.
Recombinant ADAMTS-13: first-in-human pharmacokinetics and safety in congenital thrombotic thrombocytopenic purpura.
Blood
; 130(19): 2055-2063, 2017 11 09.
Artigo
em Inglês
| MEDLINE | ID: mdl-28912376
16.
Concizumab restores thrombin generation potential in patients with haemophilia: Pharmacokinetic/pharmacodynamic modelling results of concizumab phase 1/1b data.
Haemophilia
; 25(1): 60-66, 2019 Jan.
Artigo
em Inglês
| MEDLINE | ID: mdl-30408848
17.
The effect of emicizumab prophylaxis on health-related outcomes in persons with haemophilia A with inhibitors: HAVEN 1 Study.
Haemophilia
; 25(1): 33-44, 2019 Jan.
Artigo
em Inglês
| MEDLINE | ID: mdl-30427582
18.
Pharmacokinetic parameters of recombinant factor IX Fc fusion protein are not influenced by factor IX antigen levels in subjects from the Phase 3 B-LONG trial.
Haemophilia
; 29(1): 404-407, 2023 Jan.
Artigo
em Inglês
| MEDLINE | ID: mdl-36548200
19.
Prevalence of COVID-19 related hospitalizations and mortality in adults aged ≥40 years with haemophilia: A survey from Europe.
Haemophilia
; 29(3): 913-916, 2023 05.
Artigo
em Inglês
| MEDLINE | ID: mdl-36802089
20.
Fostamatinib for the treatment of adult persistent and chronic immune thrombocytopenia: Results of two phase 3, randomized, placebo-controlled trials.
Am J Hematol
; 93(7): 921-930, 2018 07.
Artigo
em Inglês
| MEDLINE | ID: mdl-29696684