Detalhe da pesquisa
1.
Genetic Inactivation of CD33 in Hematopoietic Stem Cells to Enable CAR T Cell Immunotherapy for Acute Myeloid Leukemia.
Cell
; 173(6): 1439-1453.e19, 2018 05 31.
Artigo
em Inglês
| MEDLINE | ID: mdl-29856956
2.
Chromothriptic cure of WHIM syndrome.
Cell
; 160(4): 686-699, 2015 Feb 12.
Artigo
em Inglês
| MEDLINE | ID: mdl-25662009
3.
The Spectrum of GATA2 Deficiency Syndrome.
Blood
; 2022 Dec 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-36455197
4.
A RUNX1-FPDMM rhesus macaque model reproduces the human phenotype and predicts challenges to curative gene therapies.
Blood
; 2022 Nov 02.
Artigo
em Inglês
| MEDLINE | ID: mdl-36322931
5.
A macaque clonal hematopoiesis model demonstrates expansion of TET2-disrupted clones and utility for testing interventions.
Blood
; 140(16): 1774-1789, 2022 10 20.
Artigo
em Inglês
| MEDLINE | ID: mdl-35714307
6.
Translation of cytoplasmic UBA1 contributes to VEXAS syndrome pathogenesis.
Blood
; 140(13): 1496-1506, 2022 09 29.
Artigo
em Inglês
| MEDLINE | ID: mdl-35793467
7.
International Consensus Classification of Myeloid Neoplasms and Acute Leukemias: integrating morphologic, clinical, and genomic data.
Blood
; 140(11): 1200-1228, 2022 09 15.
Artigo
em Inglês
| MEDLINE | ID: mdl-35767897
8.
Plerixafor for the Treatment of WHIM Syndrome.
N Engl J Med
; 380(2): 163-170, 2019 01 10.
Artigo
em Inglês
| MEDLINE | ID: mdl-30625055
9.
SASH3 variants cause a novel form of X-linked combined immunodeficiency with immune dysregulation.
Blood
; 138(12): 1019-1033, 2021 09 23.
Artigo
em Inglês
| MEDLINE | ID: mdl-33876203
10.
Donor source and post-transplantation cyclophosphamide influence outcome in allogeneic stem cell transplantation for GATA2 deficiency.
Br J Haematol
; 196(1): 169-178, 2022 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-34580862
11.
Treatment optimization and genomic outcomes in refractory severe aplastic anemia treated with eltrombopag.
Blood
; 133(24): 2575-2585, 2019 06 13.
Artigo
em Inglês
| MEDLINE | ID: mdl-30992268
12.
Long-term eltrombopag for bone marrow failure depletes iron.
Am J Hematol
; 97(6): 791-801, 2022 06 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-35312200
13.
Eltrombopag Added to Standard Immunosuppression for Aplastic Anemia.
N Engl J Med
; 376(16): 1540-1550, 2017 04 20.
Artigo
em Inglês
| MEDLINE | ID: mdl-28423296
14.
Depth and durability of response to ibrutinib in CLL: 5-year follow-up of a phase 2 study.
Blood
; 131(21): 2357-2366, 2018 05 24.
Artigo
em Inglês
| MEDLINE | ID: mdl-29483101
15.
Venetoclax/decitabine for a pediatric patient with chronic myelomonocytic leukemia.
Pediatr Blood Cancer
; 68(3): e28865, 2021 03.
Artigo
em Inglês
| MEDLINE | ID: mdl-33369023
16.
Aberrant Clonal Hematopoiesis following Lentiviral Vector Transduction of HSPCs in a Rhesus Macaque.
Mol Ther
; 27(6): 1074-1086, 2019 06 05.
Artigo
em Inglês
| MEDLINE | ID: mdl-31023523
17.
The distribution of T-cell subsets and the expression of immune checkpoint receptors and ligands in patients with newly diagnosed and relapsed acute myeloid leukemia.
Cancer
; 125(9): 1470-1481, 2019 05 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-30500073
18.
Adaptive NK cells can persist in patients with GATA2 mutation depleted of stem and progenitor cells.
Blood
; 129(14): 1927-1939, 2017 04 06.
Artigo
em Inglês
| MEDLINE | ID: mdl-28209719
19.
Eltrombopag monotherapy can improve hematopoiesis in patients with low to intermediate risk-1 myelodysplastic syndrome.
Haematologica
; 105(12): 2785-2794, 2020 12 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-33256377
20.
Differential processing of high-molecular-weight kininogen during normal pregnancy.
Rapid Commun Mass Spectrom
; 34 Suppl 1: e8552, 2020 Apr.
Artigo
em Inglês
| MEDLINE | ID: mdl-31412146