Long-Term Galsulfase Treatment Associated With Improved Survival of Patients With Mucopolysaccharidosis VI (Maroteaux-Lamy Syndrome): 15-Year Follow-Up From the Survey Study

Quartel, Adrian; Harmatz, Paul R.; Lampe, Christina; Guffon, Nathalie; Ketteridge, David; Leão-Teles, Elisa; Jones, Simon A.; Giugliani, Roberto.
J. inborn errors metab. screen ; 6: e170025, 2018. tab, graf
Artigo em Inglês | LILACS-Express | ID: biblio-1090972

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