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Immune response to intrathecal enzyme replacement therapy in mucopolysaccharidosis I patients.
Vera, Moin; Le, Steven; Kan, Shih-Hsin; Garban, Hermes; Naylor, David; Mlikotic, Anton; Kaitila, Ilkka; Harmatz, Paul; Chen, Agnes; Dickson, Patricia.
Afiliação
  • Vera M; Department of Pediatrics, Los Angeles Biomedical Research Institute, Harbor-UCLA Medical Center, Torrance, California.
  • Le S; Department of Pediatrics, Los Angeles Biomedical Research Institute, Harbor-UCLA Medical Center, Torrance, California.
  • Kan SH; Department of Pediatrics, Los Angeles Biomedical Research Institute, Harbor-UCLA Medical Center, Torrance, California.
  • Garban H; Department of Internal Medicine, Los Angeles Biomedical Research Institute, Harbor-UCLA Medical Center, Torrance, California.
  • Naylor D; Department of Neurology, Los Angeles Biomedical Research Institute, Harbor-UCLA Medical Center, Torrance, California.
  • Mlikotic A; Department of Radiology, Los Angeles Biomedical Research Institute, Harbor-UCLA Medical Center, Torrance, California.
  • Kaitila I; Departments of Medical Genetics and Pediatrics, Helsinki University Central Hospital and University of Helsinki, Helsinki, Finland.
  • Harmatz P; Department of Pediatrics, Children's Hospital and Research Center Oakland, Oakland, California.
  • Chen A; Department of Pediatrics, Los Angeles Biomedical Research Institute, Harbor-UCLA Medical Center, Torrance, California.
  • Dickson P; Department of Pediatrics, Los Angeles Biomedical Research Institute, Harbor-UCLA Medical Center, Torrance, California.
Pediatr Res ; 74(6): 712-20, 2013 Dec.
Article em En | MEDLINE | ID: mdl-24002329

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Mucopolissacaridose I / Iduronidase Limite: Adult / Child, preschool / Female / Humans / Infant / Male Idioma: En Ano de publicação: 2013 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Mucopolissacaridose I / Iduronidase Limite: Adult / Child, preschool / Female / Humans / Infant / Male Idioma: En Ano de publicação: 2013 Tipo de documento: Article