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Somatropin treatment of spinal muscular atrophy: a placebo-controlled, double-blind crossover pilot study.
Kirschner, J; Schorling, D; Hauschke, D; Rensing-Zimmermann, C; Wein, U; Grieben, U; Schottmann, G; Schara, U; Konrad, K; Müller-Felber, W; Thiele, S; Wilichowski, E; Hobbiebrunken, E; Stettner, G M; Korinthenberg, R.
Afiliação
  • Kirschner J; Department of Neuropaediatrics and Muscle Disorders, University Medical Center, Freiburg, Germany. Electronic address: janbernd.kirschner@uniklinik-freiburg.de.
  • Schorling D; Department of Neuropaediatrics and Muscle Disorders, University Medical Center, Freiburg, Germany.
  • Hauschke D; Institute of Medical Biometry and Medical Informatics, University of Freiburg, Germany.
  • Rensing-Zimmermann C; Department of Neuropaediatrics and Muscle Disorders, University Medical Center, Freiburg, Germany.
  • Wein U; Department of Neuropaediatrics and Muscle Disorders, University Medical Center, Freiburg, Germany.
  • Grieben U; Department of Neuropaediatrics, Charité University Medical School, Berlin, Germany.
  • Schottmann G; Department of Neuropaediatrics, Charité University Medical School, Berlin, Germany.
  • Schara U; Department of Paediatric Neurology, University Hospital Essen, Germany.
  • Konrad K; Department of Paediatric Endocinology, University Hospital Essen, Germany.
  • Müller-Felber W; Department of Paediatric Neurology and Developmental Medicine, Dr. Von Hauner Children's Hospital, München, Germany.
  • Thiele S; Department of Paediatric Neurology and Developmental Medicine, Dr. Von Hauner Children's Hospital, München, Germany.
  • Wilichowski E; Department of Paediatrics and Paediatric Neurology, Georg August University, Göttingen, Germany.
  • Hobbiebrunken E; Department of Paediatrics and Paediatric Neurology, Georg August University, Göttingen, Germany.
  • Stettner GM; Department of Paediatrics and Paediatric Neurology, Georg August University, Göttingen, Germany.
  • Korinthenberg R; Department of Neuropaediatrics and Muscle Disorders, University Medical Center, Freiburg, Germany.
Neuromuscul Disord ; 24(2): 134-42, 2014 Feb.
Article em En | MEDLINE | ID: mdl-24300782

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Atrofias Musculares Espinais da Infância / Hormônio do Crescimento Humano / Terapia de Reposição Hormonal Tipo de estudo: Clinical_trials Limite: Adolescent / Adult / Child / Female / Humans / Male Idioma: En Ano de publicação: 2014 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Atrofias Musculares Espinais da Infância / Hormônio do Crescimento Humano / Terapia de Reposição Hormonal Tipo de estudo: Clinical_trials Limite: Adolescent / Adult / Child / Female / Humans / Male Idioma: En Ano de publicação: 2014 Tipo de documento: Article