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Efficacy and safety of deferiprone for the treatment of pantothenate kinase-associated neurodegeneration (PKAN) and neurodegeneration with brain iron accumulation (NBIA): results from a four years follow-up.
Cossu, Giovanni; Abbruzzese, Giovanni; Matta, Gildo; Murgia, Daniela; Melis, Maurizio; Ricchi, Valeria; Galanello, Renzo; Barella, Susanna; Origa, Raffaella; Balocco, Manuela; Pelosin, Elisa; Marchese, Roberta; Ruffinengo, Uberto; Forni, Gian Luca.
Afiliação
  • Cossu G; Neurology Department, "G. Brotzu" General Hospital, Cagliari, Italy. Electronic address: giovannicossu@aob.it.
  • Abbruzzese G; Department of Neurosciences, University of Genoa, Italy.
  • Matta G; Radiology Department, "G. Brotzu" General Hospital, Cagliari, Italy.
  • Murgia D; Neurology Department, "G. Brotzu" General Hospital, Cagliari, Italy.
  • Melis M; Neurology Department, "G. Brotzu" General Hospital, Cagliari, Italy.
  • Ricchi V; Neurology Department, "G. Brotzu" General Hospital, Cagliari, Italy.
  • Galanello R; Ospedale Regionale Microcitemia, University of Cagliari, Cagliari, Italy.
  • Barella S; Ospedale Regionale Microcitemia, University of Cagliari, Cagliari, Italy.
  • Origa R; Ospedale Regionale Microcitemia, University of Cagliari, Cagliari, Italy.
  • Balocco M; Centro della Microcitemia e Anemie Congenite-Haematology, Galliera Hospital, Genoa, Italy.
  • Pelosin E; Department of Neurosciences, University of Genoa, Italy.
  • Marchese R; Department of Neurosciences, University of Genoa, Italy.
  • Ruffinengo U; Neuroradiology Unit, Galliera Hospital, Genoa, Italy.
  • Forni GL; Centro della Microcitemia e Anemie Congenite-Haematology, Galliera Hospital, Genoa, Italy.
Parkinsonism Relat Disord ; 20(6): 651-4, 2014 Jun.
Article em En | MEDLINE | ID: mdl-24661465

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Piridonas / Quelantes de Ferro / Distrofias Neuroaxonais / Distúrbios do Metabolismo do Ferro / Neurodegeneração Associada a Pantotenato-Quinase Tipo de estudo: Diagnostic_studies / Observational_studies / Prognostic_studies / Risk_factors_studies Limite: Adult / Female / Humans / Male / Middle aged Idioma: En Ano de publicação: 2014 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Piridonas / Quelantes de Ferro / Distrofias Neuroaxonais / Distúrbios do Metabolismo do Ferro / Neurodegeneração Associada a Pantotenato-Quinase Tipo de estudo: Diagnostic_studies / Observational_studies / Prognostic_studies / Risk_factors_studies Limite: Adult / Female / Humans / Male / Middle aged Idioma: En Ano de publicação: 2014 Tipo de documento: Article