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European Medicines Agency review of ataluren for the treatment of ambulant patients aged 5 years and older with Duchenne muscular dystrophy resulting from a nonsense mutation in the dystrophin gene.
Haas, Manuel; Vlcek, Viktor; Balabanov, Pavel; Salmonson, Tomas; Bakchine, Serge; Markey, Greg; Weise, Martina; Schlosser-Weber, Gabriele; Brohmann, Henning; Yerro, Concepcion Prieto; Mendizabal, Macarena Rodriguez; Stoyanova-Beninska, Violeta; Hillege, Hans L.
Afiliação
  • Haas M; European Medicines Agency, London, United Kingdom. Electronic address: manuel.haas@ema.europa.eu.
  • Vlcek V; European Medicines Agency, London, United Kingdom.
  • Balabanov P; European Medicines Agency, London, United Kingdom.
  • Salmonson T; Läkemedelsverket, Medical Products Agency, Uppsala, Sweden.
  • Bakchine S; Hôpital Maison Blanche, CHU de Reims, Reims, France.
  • Markey G; Medicines and Healthcare Products Regulatory Agency, London, United Kingdom.
  • Weise M; Bundesinstitut für Arzneimittel und Medizinprodukte, Bonn, Germany.
  • Schlosser-Weber G; Bundesinstitut für Arzneimittel und Medizinprodukte, Bonn, Germany.
  • Brohmann H; Bundesinstitut für Arzneimittel und Medizinprodukte, Bonn, Germany.
  • Yerro CP; Agencia Española de Medicamentos y Productos Sanitarios, Madrid, Spain.
  • Mendizabal MR; Agencia Española de Medicamentos y Productos Sanitarios, Madrid, Spain.
  • Stoyanova-Beninska V; Medicines Evaluation Board, Utrecht, The Netherlands.
  • Hillege HL; Medicines Evaluation Board, Utrecht, The Netherlands.
Neuromuscul Disord ; 25(1): 5-13, 2015 Jan.
Article em En | MEDLINE | ID: mdl-25497400

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Oxidiazóis / Distrofina / Aprovação de Drogas / Códon sem Sentido / Distrofia Muscular de Duchenne Tipo de estudo: Clinical_trials Limite: Adolescent / Adult / Child / Child, preschool / Humans / Male Idioma: En Ano de publicação: 2015 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Oxidiazóis / Distrofina / Aprovação de Drogas / Códon sem Sentido / Distrofia Muscular de Duchenne Tipo de estudo: Clinical_trials Limite: Adolescent / Adult / Child / Child, preschool / Humans / Male Idioma: En Ano de publicação: 2015 Tipo de documento: Article