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Mucopolysaccharidosis-like phenotype in feline Sandhoff disease and partial correction after AAV gene therapy.
Gray-Edwards, Heather L; Brunson, Brandon L; Holland, Merrilee; Hespel, Adrien-Maxence; Bradbury, Allison M; McCurdy, Victoria J; Beadlescomb, Patricia M; Randle, Ashley N; Salibi, Nouha; Denney, Thomas S; Beyers, Ronald J; Johnson, Aime K; Voyles, Meredith L; Montgomery, Ronald D; Wilson, Diane U; Hudson, Judith A; Cox, Nancy R; Baker, Henry J; Sena-Esteves, Miguel; Martin, Douglas R.
Afiliação
  • Gray-Edwards HL; Scott-Ritchey Research Center, College of Veterinary Medicine, Auburn University, Auburn, AL, USA. Electronic address: grayhea@auburn.edu.
  • Brunson BL; Department of Anatomy, Physiology & Pharmacology, College of Veterinary Medicine, Auburn University, Auburn, AL, USA.
  • Holland M; Department of Clinical Sciences, College of Veterinary Medicine, Auburn University, Auburn, AL, USA.
  • Hespel AM; Department of Clinical Sciences, College of Veterinary Medicine, Auburn University, Auburn, AL, USA.
  • Bradbury AM; Scott-Ritchey Research Center, College of Veterinary Medicine, Auburn University, Auburn, AL, USA; Department of Anatomy, Physiology & Pharmacology, College of Veterinary Medicine, Auburn University, Auburn, AL, USA.
  • McCurdy VJ; Scott-Ritchey Research Center, College of Veterinary Medicine, Auburn University, Auburn, AL, USA; Department of Anatomy, Physiology & Pharmacology, College of Veterinary Medicine, Auburn University, Auburn, AL, USA.
  • Beadlescomb PM; Scott-Ritchey Research Center, College of Veterinary Medicine, Auburn University, Auburn, AL, USA; Department of Anatomy, Physiology & Pharmacology, College of Veterinary Medicine, Auburn University, Auburn, AL, USA.
  • Randle AN; Scott-Ritchey Research Center, College of Veterinary Medicine, Auburn University, Auburn, AL, USA.
  • Salibi N; MR R&D Siemens Healthcare, Malvern, PA, USA; Auburn University MRI Research Center, Auburn, AL, USA.
  • Denney TS; Auburn University MRI Research Center, Auburn, AL, USA; Department of Electrical and Computer Engineering, Auburn University, Auburn, AL, USA.
  • Beyers RJ; Auburn University MRI Research Center, Auburn, AL, USA.
  • Johnson AK; Department of Clinical Sciences, College of Veterinary Medicine, Auburn University, Auburn, AL, USA.
  • Voyles ML; Department of Clinical Sciences, College of Veterinary Medicine, Auburn University, Auburn, AL, USA.
  • Montgomery RD; Department of Clinical Sciences, College of Veterinary Medicine, Auburn University, Auburn, AL, USA.
  • Wilson DU; Scott-Ritchey Research Center, College of Veterinary Medicine, Auburn University, Auburn, AL, USA; Department of Clinical Sciences, College of Veterinary Medicine, Auburn University, Auburn, AL, USA.
  • Hudson JA; Department of Clinical Sciences, College of Veterinary Medicine, Auburn University, Auburn, AL, USA.
  • Cox NR; Scott-Ritchey Research Center, College of Veterinary Medicine, Auburn University, Auburn, AL, USA; Department of Pathobiology, College of Veterinary Medicine, Auburn University, Auburn, AL, USA.
  • Baker HJ; Scott-Ritchey Research Center, College of Veterinary Medicine, Auburn University, Auburn, AL, USA; Department of Pathobiology, College of Veterinary Medicine, Auburn University, Auburn, AL, USA.
  • Sena-Esteves M; Department of Neurology and Gene Therapy Center, University of Massachusetts Medical School, Worcester, MA, USA.
  • Martin DR; Scott-Ritchey Research Center, College of Veterinary Medicine, Auburn University, Auburn, AL, USA; Department of Anatomy, Physiology & Pharmacology, College of Veterinary Medicine, Auburn University, Auburn, AL, USA.
Mol Genet Metab ; 116(1-2): 80-7, 2015.
Article em En | MEDLINE | ID: mdl-25971245

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Doença de Sandhoff / Beta-N-Acetil-Hexosaminidases / Terapia Genética Limite: Animals / Humans Idioma: En Ano de publicação: 2015 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Doença de Sandhoff / Beta-N-Acetil-Hexosaminidases / Terapia Genética Limite: Animals / Humans Idioma: En Ano de publicação: 2015 Tipo de documento: Article