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Recapitulation of metabolic defects in a model of propionic acidemia using patient-derived primary hepatocytes.
Chapman, Kimberly A; Collado, Maria S; Figler, Robert A; Hoang, Stephen A; Armstrong, Allison J; Cui, Wanxing; Purdy, Michael; Simmers, Michael B; Yazigi, Nada A; Summar, Marshall L; Wamhoff, Brian R; Dash, Ajit.
Afiliação
  • Chapman KA; Children's National Medical Center and George Washington University, Washington, DC, United States.
  • Collado MS; HemoShear Therapeutics, Charlottesville, VA, United States.
  • Figler RA; HemoShear Therapeutics, Charlottesville, VA, United States.
  • Hoang SA; HemoShear Therapeutics, Charlottesville, VA, United States.
  • Armstrong AJ; HemoShear Therapeutics, Charlottesville, VA, United States.
  • Cui W; Georgetown University Hospital, Washington, DC, United States.
  • Purdy M; University of Virginia, Charlottesville, VA, United States.
  • Simmers MB; HemoShear Therapeutics, Charlottesville, VA, United States.
  • Yazigi NA; Georgetown University Hospital, Washington, DC, United States.
  • Summar ML; Children's National Medical Center and George Washington University, Washington, DC, United States.
  • Wamhoff BR; HemoShear Therapeutics, Charlottesville, VA, United States.
  • Dash A; HemoShear Therapeutics, Charlottesville, VA, United States.
Mol Genet Metab ; 117(3): 355-362, 2016 Mar.
Article em En | MEDLINE | ID: mdl-26740382

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Hepatócitos / Acidemia Propiônica Limite: Child / Humans Idioma: En Ano de publicação: 2016 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Hepatócitos / Acidemia Propiônica Limite: Child / Humans Idioma: En Ano de publicação: 2016 Tipo de documento: Article