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Therapeutic genome editing by combined viral and non-viral delivery of CRISPR system components in vivo.
Yin, Hao; Song, Chun-Qing; Dorkin, Joseph R; Zhu, Lihua J; Li, Yingxiang; Wu, Qiongqiong; Park, Angela; Yang, Junghoon; Suresh, Sneha; Bizhanova, Aizhan; Gupta, Ankit; Bolukbasi, Mehmet F; Walsh, Stephen; Bogorad, Roman L; Gao, Guangping; Weng, Zhiping; Dong, Yizhou; Koteliansky, Victor; Wolfe, Scot A; Langer, Robert; Xue, Wen; Anderson, Daniel G.
Afiliação
  • Yin H; David H. Koch Institute for Integrative Cancer Research, Massachusetts Institute of Technology, Cambridge, Massachusetts, USA.
  • Song CQ; RNA Therapeutics Institute, University of Massachusetts Medical School, Worcester, Massachusetts, USA.
  • Dorkin JR; Program in Molecular Medicine, University of Massachusetts Medical School, Worcester, Massachusetts, USA.
  • Zhu LJ; David H. Koch Institute for Integrative Cancer Research, Massachusetts Institute of Technology, Cambridge, Massachusetts, USA.
  • Li Y; Department of Biology, Massachusetts Institute of Technology, Cambridge, Massachusetts, USA.
  • Wu Q; Program in Molecular Medicine, University of Massachusetts Medical School, Worcester, Massachusetts, USA.
  • Park A; Department of Molecular, Cell and Cancer Biology, University of Massachusetts Medical School, Worcester, Massachusetts, USA.
  • Yang J; Program in Bioinformatics and Integrative Biology, University of Massachusetts Medical School, Worcester, Massachusetts, USA.
  • Suresh S; Department of Bioinformatics, School of Life Science and Technology, Tongji University, Shanghai, P.R. China.
  • Bizhanova A; David H. Koch Institute for Integrative Cancer Research, Massachusetts Institute of Technology, Cambridge, Massachusetts, USA.
  • Gupta A; RNA Therapeutics Institute, University of Massachusetts Medical School, Worcester, Massachusetts, USA.
  • Bolukbasi MF; David H. Koch Institute for Integrative Cancer Research, Massachusetts Institute of Technology, Cambridge, Massachusetts, USA.
  • Walsh S; David H. Koch Institute for Integrative Cancer Research, Massachusetts Institute of Technology, Cambridge, Massachusetts, USA.
  • Bogorad RL; RNA Therapeutics Institute, University of Massachusetts Medical School, Worcester, Massachusetts, USA.
  • Gao G; Department of Molecular, Cell and Cancer Biology, University of Massachusetts Medical School, Worcester, Massachusetts, USA.
  • Weng Z; Department of Molecular, Cell and Cancer Biology, University of Massachusetts Medical School, Worcester, Massachusetts, USA.
  • Dong Y; Department of Biochemistry and Molecular Pharmacology, University of Massachusetts Medical School, Worcester, Massachusetts, USA.
  • Koteliansky V; David H. Koch Institute for Integrative Cancer Research, Massachusetts Institute of Technology, Cambridge, Massachusetts, USA.
  • Wolfe SA; David H. Koch Institute for Integrative Cancer Research, Massachusetts Institute of Technology, Cambridge, Massachusetts, USA.
  • Langer R; Gene Therapy Center, University of Massachusetts Medical School, Worcester, Massachusetts, USA.
  • Xue W; Program in Bioinformatics and Integrative Biology, University of Massachusetts Medical School, Worcester, Massachusetts, USA.
  • Anderson DG; College of Pharmacy, the Ohio State University, Columbus, Ohio, USA.
Nat Biotechnol ; 34(3): 328-33, 2016 Mar.
Article em En | MEDLINE | ID: mdl-26829318

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Genoma Humano / Edição de RNA / Tirosinemias / Sistemas CRISPR-Cas Limite: Animals / Humans Idioma: En Ano de publicação: 2016 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Genoma Humano / Edição de RNA / Tirosinemias / Sistemas CRISPR-Cas Limite: Animals / Humans Idioma: En Ano de publicação: 2016 Tipo de documento: Article