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Immunological Factors in Pompe Disease Management: Clinical Experience and Implications for Newborn Screening.
Kishnani, Priya S; Kazi, Zoheb B; Berrier, Kathryn L; Dearmey, Stephanie M; Bali, Deeksha S; Rosenberg, Amy S.
Afiliação
  • Kishnani PS; Division of Medical Genetics, Department of Pediatrics, Duke University Health System, Durham, NC.
  • Kazi ZB; Division of Medical Genetics, Department of Pediatrics, Duke University Health System, Durham, NC.
  • Berrier KL; Division of Medical Genetics, Department of Pediatrics, Duke University Health System, Durham, NC.
  • Dearmey SM; Division of Medical Genetics, Department of Pediatrics, Duke University Health System, Durham, NC.
  • Bali DS; Division of Medical Genetics, Department of Pediatrics, Duke University Health System, Durham, NC.
  • Rosenberg AS; Division of Therapeutic Proteins, Office of Biotechnology Products, Center for Drug Evaluation and Research, United States Food and Drug Administration.
J Neuromuscul Dis ; 2(s1): S7, 2015.
Article em En | MEDLINE | ID: mdl-27858605
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Coleções: 01-internacional Base de dados: MEDLINE Tipo de estudo: Diagnostic_studies / Screening_studies Idioma: En Ano de publicação: 2015 Tipo de documento: Article
Buscar no Google
Coleções: 01-internacional Base de dados: MEDLINE Tipo de estudo: Diagnostic_studies / Screening_studies Idioma: En Ano de publicação: 2015 Tipo de documento: Article