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Pharmacokinetics of a novel extended half-life glycoPEGylated factor IX, nonacog beta pegol (N9-GP) in previously treated patients with haemophilia B: results from two phase 3 clinical trials.
Tiede, A; Abdul-Karim, F; Carcao, M; Persson, P; Clausen, W H O; Kearney, S; Matsushita, T; Negrier, C; Oldenburg, J; Santagostino, E; Young, G.
Afiliação
  • Tiede A; Clinic for Haematology, Haemostaseology, Oncology and Stem Cell Transplantation, Hannover Medical School, Hannover, Germany.
  • Abdul-Karim F; Hemophilia Clinic, National Blood Centre, Wilayah Persekutuan, Kuala Lumpur, Malaysia.
  • Carcao M; Division of Haematology/Oncology, Department of Paediatrics, Child Health Evaluative Sciences, Research Institute, The Hospital for Sick Children, University of Toronto, Toronto, ON, Canada.
  • Persson P; Novo Nordisk A/S, Søborg, Denmark.
  • Clausen WHO; Novo Nordisk A/S, Søborg, Denmark.
  • Kearney S; CHCMN Hemophilia and Thrombosis Center, Children's Hospital and Clinics of Minnesota, MN, USA.
  • Matsushita T; Department of Transfusion Medicine, Nagoya University Hospital, Nagoya, Japan.
  • Negrier C; Centre Regional de Traitement de l'Hemophilie, Hopital Louis Pradel, University Claude Bernard, Lyon, France.
  • Oldenburg J; Institute of Experimental Haematology and Transfusion Medicine, Bonn, Germany.
  • Santagostino E; Angelo Bianchi Bonomi Haemophilia and Thrombosis Centre, Maggiore Hospital, IRCCS Ca Granda Foundation, Milan, Italy.
  • Young G; Hemostasis and Thrombosis Center, Children's Hospital Los Angeles, Keck School of Medicine, University of Southern California, Los Angeles, CA, USA.
Haemophilia ; 23(4): 547-555, 2017 Jul.
Article em En | MEDLINE | ID: mdl-28233381

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Polietilenoglicóis / Fator IX / Hemofilia B Tipo de estudo: Prognostic_studies Limite: Adolescent / Child / Child, preschool / Humans / Male Idioma: En Ano de publicação: 2017 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Polietilenoglicóis / Fator IX / Hemofilia B Tipo de estudo: Prognostic_studies Limite: Adolescent / Child / Child, preschool / Humans / Male Idioma: En Ano de publicação: 2017 Tipo de documento: Article