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Synergistic effects of treating the spinal cord and brain in CLN1 disease.
Shyng, Charles; Nelvagal, Hemanth R; Dearborn, Joshua T; Tyynelä, Jaana; Schmidt, Robert E; Sands, Mark S; Cooper, Jonathan D.
Afiliação
  • Shyng C; Division of Oncology, Department of Medicine, Washington University School of Medicine, St. Louis, MO 63110.
  • Nelvagal HR; Department of Basic and Clinical Neuroscience, Maurice Wohl Clinical Neuroscience Institute, Institute of Psychiatry, Psychology & Neuroscience, King's College London, London SE5 9RX, United Kingdom.
  • Dearborn JT; Department of Pediatrics, Los Angeles Biomedical Research Institute, Harbor-UCLA Medical Center, University of California, Los Angeles, Torrance, CA 90502.
  • Tyynelä J; Division of Oncology, Department of Medicine, Washington University School of Medicine, St. Louis, MO 63110.
  • Schmidt RE; Institute of Biomedicine/Biochemistry, University of Helsinki, 00014 Helsinki, Finland.
  • Sands MS; Division of Neuropathology, Department of Pathology & Immunology, Washington University School of Medicine, St. Louis, MO 63110.
  • Cooper JD; Division of Oncology, Department of Medicine, Washington University School of Medicine, St. Louis, MO 63110; msands@dom.wustl.edu jonathan.cooper@labiomed.org.
Proc Natl Acad Sci U S A ; 114(29): E5920-E5929, 2017 07 18.
Article em En | MEDLINE | ID: mdl-28673981

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Medula Espinal / Tioléster Hidrolases / Encéfalo / Terapia Genética / Proteínas de Membrana / Lipofuscinoses Ceroides Neuronais Tipo de estudo: Prognostic_studies Limite: Animals / Child / Humans Idioma: En Ano de publicação: 2017 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Medula Espinal / Tioléster Hidrolases / Encéfalo / Terapia Genética / Proteínas de Membrana / Lipofuscinoses Ceroides Neuronais Tipo de estudo: Prognostic_studies Limite: Animals / Child / Humans Idioma: En Ano de publicação: 2017 Tipo de documento: Article