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Design optimization for clinical trials in early-stage manifest Huntington's disease.
Frost, Chris; Mulick, Amy; Scahill, Rachael I; Owen, Gail; Aylward, Elizabeth; Leavitt, Blair R; Durr, Alexandra; Roos, Raymund A C; Borowsky, Beth; Stout, Julie C; Reilmann, Ralf; Langbehn, Douglas R; Tabrizi, Sarah J; Sampaio, Cristina.
Afiliação
  • Frost C; Department of Medical Statistics, London School of Hygiene and Tropical Medicine, London, UK.
  • Mulick A; Department of Medical Statistics, London School of Hygiene and Tropical Medicine, London, UK.
  • Scahill RI; Huntington's Disease Centre, UCL Institute of Neurology, Department of Neurodegenerative Disease, University College London, London, UK.
  • Owen G; Huntington's Disease Centre, UCL Institute of Neurology, Department of Neurodegenerative Disease, University College London, London, UK.
  • Aylward E; Center for Integrative Brain Research, Seattle Children's Research Institute, Seattle, Washington, USA.
  • Leavitt BR; Department of Medical Genetics, University of British Columbia, Vancouver, British Columbia, Canada.
  • Durr A; Brain and Spine Institute, INSERM U1127, Centre National de la Recherche Scientifique, UMR7225, Sorbonne Universités, University Pierre and Marie Curie, Paris VI UMR_S1127, Paris, France.
  • Roos RAC; Assistance Publique - Hôpitaux de Paris, Genetic Department, Pitié -Salpêtrière University Hospital, Paris, France.
  • Borowsky B; Department of Neurology, Leiden University Medical Centre, Leiden, The Netherlands.
  • Stout JC; CHDI Management, CHDI Foundation, Princeton, New Jersey, USA.
  • Reilmann R; Clinical Development, Neurodegenerative Diseases, Teva Pharmaceuticals, Malvern Pennsylvania, USA.
  • Langbehn DR; School of Psychological Sciences, Monash University, Melbourne, Victoria, Australia.
  • Tabrizi SJ; George Huntington Institute, Muenster, Germany.
  • Sampaio C; Institute for Clinical Radiology, University of Muenster, Muenster, Germany.
Mov Disord ; 32(11): 1610-1619, 2017 Nov.
Article em En | MEDLINE | ID: mdl-28906031

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Projetos de Pesquisa / Núcleo Caudado / Ensaios Clínicos Controlados Aleatórios como Assunto / Avaliação de Resultados em Cuidados de Saúde / Doença de Huntington Tipo de estudo: Clinical_trials / Observational_studies / Prognostic_studies / Risk_factors_studies Limite: Adult / Female / Humans / Male / Middle aged Idioma: En Ano de publicação: 2017 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Projetos de Pesquisa / Núcleo Caudado / Ensaios Clínicos Controlados Aleatórios como Assunto / Avaliação de Resultados em Cuidados de Saúde / Doença de Huntington Tipo de estudo: Clinical_trials / Observational_studies / Prognostic_studies / Risk_factors_studies Limite: Adult / Female / Humans / Male / Middle aged Idioma: En Ano de publicação: 2017 Tipo de documento: Article