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Prevalence and management of iron overload in pyruvate kinase deficiency: report from the Pyruvate Kinase Deficiency Natural History Study.
van Beers, Eduard J; van Straaten, Stephanie; Morton, D Holmes; Barcellini, Wilma; Eber, Stefan W; Glader, Bertil; Yaish, Hassan M; Chonat, Satheesh; Kwiatkowski, Janet L; Rothman, Jennifer A; Sharma, Mukta; Neufeld, Ellis J; Sheth, Sujit; Despotovic, Jenny M; Kollmar, Nina; Pospísilová, Dagmar; Knoll, Christine M; Kuo, Kevin; Pastore, Yves D; Thompson, Alexis A; Newburger, Peter E; Ravindranath, Yaddanapudi; Wang, Winfred C; Wlodarski, Marcin W; Wang, Heng; Holzhauer, Susanne; Breakey, Vicky R; Verhovsek, Madeleine; Kunz, Joachim; McNaull, Melissa A; Rose, Melissa J; Bradeen, Heather A; Addonizio, Kathryn; Li, Anran; Al-Sayegh, Hasan; London, Wendy B; Grace, Rachael F.
Afiliação
  • van Beers EJ; Van Creveldkliniek, University Medical Centre Utrecht, University of Utrecht, the Netherlands.
  • van Straaten S; Van Creveldkliniek, University Medical Centre Utrecht, University of Utrecht, the Netherlands.
  • Morton DH; Central Pennsylvania Clinic for Special Children & Adults, Belleville, PA, USA Lancaster General Hospital, Lancaster, PA, USA.
  • Barcellini W; Fondazione IRCCS Ca' Granda, Ospedale Maggiore Policlinico, Milan, Italy.
  • Eber SW; Schwerpunktpraxis für Pädiatrische Hämatologie-Onkologie and Children's Hospital, Technical University, Munich, Germany.
  • Glader B; Lucile Packard Children's Hospital, Stanford University, Palo Alto, CA, USA.
  • Yaish HM; Primary Children's Hospital, University of Utah, Salt Lake City, UT, USA.
  • Chonat S; Emory University School of Medicine, Aflac Cancer and Blood Disorders Center, Children's Healthcare of Atlanta, GA, USA.
  • Kwiatkowski JL; Children's Hospital of Philadelphia and Perelman School of Medicine of the University of Pennsylvania, Philadelphia, PA, USA.
  • Rothman JA; Duke University Medical Center, Durham, NC, USA.
  • Sharma M; Children's Mercy Hospital, University of Missouri, Kansas City, MO, USA.
  • Neufeld EJ; St. Jude Children's Research Hospital, Memphis, TN, USA.
  • Sheth S; Weill Cornell Medical College, New York Presbyterian Hospital, NY, USA.
  • Despotovic JM; Texas Children's Hematology Center, Baylor College of Medicine, Houston, TX, USA.
  • Kollmar N; Klinikum Kassel GmbH, Germany.
  • Pospísilová D; Fakultni nemocnice Olomouc, Czech Republic.
  • Knoll CM; Phoenix Children's Hospital, AZ, USA.
  • Kuo K; University of Toronto, University Health Network, ON, Canada.
  • Pastore YD; CHU Sainte-Justine, Montreal, QC, Canada.
  • Thompson AA; Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago, IL, USA.
  • Newburger PE; University of Massachusetts Medical School, Worcester, MA, USA.
  • Ravindranath Y; Children's Hospital of Michigan, Wayne State University School of Medicine, Detroit, MI, USA.
  • Wang WC; St. Jude Children's Research Hospital, Memphis, TN, USA.
  • Wlodarski MW; Department of Pediatrics and Adolescent Medicine, Division of Pediatric Hematology and Oncology, Medical Center, Faculty of Medicine, University of Freiburg, Germany.
  • Wang H; DDC Clinic for Special Needs Children, Middlefield, OH, USA.
  • Holzhauer S; Charite, Berlin, Germany.
  • Breakey VR; McMaster University, Hamilton, ON, Canada.
  • Verhovsek M; McMaster University, Hamilton, ON, Canada.
  • Kunz J; Zentrum für Kinder-und Jugendmedizin,University of Heidelberg, Heidelberg, Germany.
  • McNaull MA; University of Mississippi Medical Center, Jackson, MS, USA.
  • Rose MJ; Nationwide Children's Hospital,The Ohio State University College of Medicine, Columbus, OH, USA.
  • Bradeen HA; The University of Vermont Children's Hospital, Burlington, VT, USA.
  • Addonizio K; Dana-Farber Boston Children's Cancer and Blood Disorder Center, Boston, MA, USA.
  • Li A; Dana-Farber Boston Children's Cancer and Blood Disorder Center, Boston, MA, USA.
  • Al-Sayegh H; Dana-Farber Boston Children's Cancer and Blood Disorder Center, Boston, MA, USA.
  • London WB; Dana-Farber Boston Children's Cancer and Blood Disorder Center, Boston, MA, USA.
  • Grace RF; Dana-Farber Boston Children's Cancer and Blood Disorder Center, Boston, MA, USA rachael.grace@childrens.harvard.edu.
Haematologica ; 104(2): e51-e53, 2019 02.
Article em En | MEDLINE | ID: mdl-30213831

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Piruvato Quinase / Sobrecarga de Ferro Tipo de estudo: Diagnostic_studies / Prevalence_studies / Risk_factors_studies Limite: Humans Idioma: En Ano de publicação: 2019 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Piruvato Quinase / Sobrecarga de Ferro Tipo de estudo: Diagnostic_studies / Prevalence_studies / Risk_factors_studies Limite: Humans Idioma: En Ano de publicação: 2019 Tipo de documento: Article