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Toxicology and Pharmacology of an AAV Vector Expressing Codon-Optimized RPGR in RPGR-Deficient Rd9 Mice.
Song, Chunjuan; Conlon, Thomas J; Deng, Wen-Tao; Coleman, Kirsten E; Zhu, Ping; Plummer, Cayrn; Mandapati, Savitri; Van Hoosear, Mailin; Green, Kari B; Sonnentag, Peter; Sharma, Alok K; Timmers, Adrian; Robinson, Paulette M; Knop, David R; Hauswirth, William W; Chulay, Jeffrey D; Shearman, Mark S; Ye, Guo-Jie.
Afiliação
  • Song C; 1 Applied Genetic Technologies Corporation (AGTC), Alachua, FL.
  • Conlon TJ; 2 CR Scientific and Compliance Consulting LLC, Gainesville, FL.
  • Deng WT; 3 Department of Ophthalmology, University of Florida, Gainesville, FL.
  • Coleman KE; 3 Department of Ophthalmology, University of Florida, Gainesville, FL.
  • Zhu P; 3 Department of Ophthalmology, University of Florida, Gainesville, FL.
  • Plummer C; 3 Department of Ophthalmology, University of Florida, Gainesville, FL.
  • Mandapati S; 1 Applied Genetic Technologies Corporation (AGTC), Alachua, FL.
  • Van Hoosear M; 1 Applied Genetic Technologies Corporation (AGTC), Alachua, FL.
  • Green KB; 4 Department of Chemistry, University of Florida, Gainesville, FL.
  • Sonnentag P; 5 Covance Inc, Madison, WI.
  • Sharma AK; 5 Covance Inc, Madison, WI.
  • Timmers A; 1 Applied Genetic Technologies Corporation (AGTC), Alachua, FL.
  • Robinson PM; 1 Applied Genetic Technologies Corporation (AGTC), Alachua, FL.
  • Knop DR; 1 Applied Genetic Technologies Corporation (AGTC), Alachua, FL.
  • Hauswirth WW; 3 Department of Ophthalmology, University of Florida, Gainesville, FL.
  • Chulay JD; 1 Applied Genetic Technologies Corporation (AGTC), Alachua, FL.
  • Shearman MS; 1 Applied Genetic Technologies Corporation (AGTC), Alachua, FL.
  • Ye GJ; 1 Applied Genetic Technologies Corporation (AGTC), Alachua, FL.
Hum Gene Ther Clin Dev ; 29(4): 188-197, 2018 12.
Article em En | MEDLINE | ID: mdl-30280954

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Terapia Genética / Proteínas de Transporte / Retinose Pigmentar / Dependovirus / Receptor Quinase 1 Acoplada a Proteína G / Proteínas do Olho Tipo de estudo: Evaluation_studies Limite: Animals Idioma: En Ano de publicação: 2018 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Terapia Genética / Proteínas de Transporte / Retinose Pigmentar / Dependovirus / Receptor Quinase 1 Acoplada a Proteína G / Proteínas do Olho Tipo de estudo: Evaluation_studies Limite: Animals Idioma: En Ano de publicação: 2018 Tipo de documento: Article