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Association of immune response with efficacy and safety outcomes in adults with phenylketonuria administered pegvaliase in phase 3 clinical trials.
Gupta, Soumi; Lau, Kelly; Harding, Cary O; Shepherd, Gillian; Boyer, Ryan; Atkinson, John P; Knight, Vijaya; Olbertz, Joy; Larimore, Kevin; Gu, Zhonghu; Li, Mingjin; Rosen, Orli; Zoog, Stephen J; Weng, Haoling H; Schweighardt, Becky.
Afiliação
  • Gupta S; BioMarin Pharmaceutical Inc., 105 Digital Dr, Novato, CA 94949, United States. Electronic address: soumi.gupta@bmrn.com.
  • Lau K; BioMarin Pharmaceutical Inc., 105 Digital Dr, Novato, CA 94949, United States.
  • Harding CO; Oregon Health & Science University, 3181 SW Sam Jackson Park Rd, Portland, OR 97239, United States.
  • Shepherd G; Weill Medical College of Cornell University, 47 East 91st St, New York, NY 10128, United States.
  • Boyer R; BioMarin Pharmaceutical Inc., 105 Digital Dr, Novato, CA 94949, United States.
  • Atkinson JP; Washington University School of Medicine, Campus Box 8045, 660 S. Euclid Ave, St. Louis, MO 63110, United States.
  • Knight V; National Jewish Health Advanced Diagnostic Laboratories, 1400 Jackson St, Denver, CO 80206, United States.
  • Olbertz J; BioMarin Pharmaceutical Inc., 105 Digital Dr, Novato, CA 94949, United States.
  • Larimore K; BioMarin Pharmaceutical Inc., 105 Digital Dr, Novato, CA 94949, United States.
  • Gu Z; BioMarin Pharmaceutical Inc., 105 Digital Dr, Novato, CA 94949, United States.
  • Li M; BioMarin Pharmaceutical Inc., 105 Digital Dr, Novato, CA 94949, United States.
  • Rosen O; BioMarin Pharmaceutical Inc., 105 Digital Dr, Novato, CA 94949, United States.
  • Zoog SJ; BioMarin Pharmaceutical Inc., 105 Digital Dr, Novato, CA 94949, United States.
  • Weng HH; BioMarin Pharmaceutical Inc., 105 Digital Dr, Novato, CA 94949, United States.
  • Schweighardt B; BioMarin Pharmaceutical Inc., 105 Digital Dr, Novato, CA 94949, United States.
EBioMedicine ; 37: 366-373, 2018 Nov.
Article em En | MEDLINE | ID: mdl-30366815

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Fenilalanina Amônia-Liase / Fenilcetonúrias / Proteínas Recombinantes / Hipersensibilidade a Drogas / Anticorpos / Complexo Antígeno-Anticorpo Tipo de estudo: Clinical_trials / Risk_factors_studies Limite: Adult / Female / Humans / Male Idioma: En Ano de publicação: 2018 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Fenilalanina Amônia-Liase / Fenilcetonúrias / Proteínas Recombinantes / Hipersensibilidade a Drogas / Anticorpos / Complexo Antígeno-Anticorpo Tipo de estudo: Clinical_trials / Risk_factors_studies Limite: Adult / Female / Humans / Male Idioma: En Ano de publicação: 2018 Tipo de documento: Article