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Dual AAV-mediated gene therapy restores hearing in a DFNB9 mouse model.
Akil, Omar; Dyka, Frank; Calvet, Charlotte; Emptoz, Alice; Lahlou, Ghizlene; Nouaille, Sylvie; Boutet de Monvel, Jacques; Hardelin, Jean-Pierre; Hauswirth, William W; Avan, Paul; Petit, Christine; Safieddine, Saaid; Lustig, Lawrence R.
Afiliação
  • Akil O; Department of Otolaryngology-Head and Neck Surgery, University of California, San Francisco, CA.
  • Dyka F; Department of Ophthalmology, College of Medicine, University of Florida, Gainesville, FL 32610.
  • Calvet C; Genetics and Physiology of Hearing Laboratory, Institut Pasteur, 75015 Paris, France.
  • Emptoz A; Inserm Unité Mixte de Recherche en Santé 1120, Institut National de la Santé et de la Recherche Médicale, 75015 Paris, France.
  • Lahlou G; Complexité du Vivant, Sorbonne Universités, F-75005 Paris, France.
  • Nouaille S; Genetics and Physiology of Hearing Laboratory, Institut Pasteur, 75015 Paris, France.
  • Boutet de Monvel J; Inserm Unité Mixte de Recherche en Santé 1120, Institut National de la Santé et de la Recherche Médicale, 75015 Paris, France.
  • Hardelin JP; Complexité du Vivant, Sorbonne Universités, F-75005 Paris, France.
  • Hauswirth WW; Genetics and Physiology of Hearing Laboratory, Institut Pasteur, 75015 Paris, France.
  • Avan P; Inserm Unité Mixte de Recherche en Santé 1120, Institut National de la Santé et de la Recherche Médicale, 75015 Paris, France.
  • Petit C; Complexité du Vivant, Sorbonne Universités, F-75005 Paris, France.
  • Safieddine S; Genetics and Physiology of Hearing Laboratory, Institut Pasteur, 75015 Paris, France.
  • Lustig LR; Inserm Unité Mixte de Recherche en Santé 1120, Institut National de la Santé et de la Recherche Médicale, 75015 Paris, France.
Proc Natl Acad Sci U S A ; 116(10): 4496-4501, 2019 03 05.
Article em En | MEDLINE | ID: mdl-30782832

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Terapia Genética / Dependovirus / Surdez / Proteínas de Membrana Limite: Animals / Humans Idioma: En Ano de publicação: 2019 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Terapia Genética / Dependovirus / Surdez / Proteínas de Membrana Limite: Animals / Humans Idioma: En Ano de publicação: 2019 Tipo de documento: Article