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Effectivenesss of ivacaftor in severe cystic fibrosis patients and non-G551D gating mutations.
Salvatore, Donatello; Carnovale, Vincenzo; Iacotucci, Paola; Braggion, Cesare; Castellani, Carlo; Cimino, Giuseppe; Colangelo, Carmela; Francalanci, Michela; Leonetti, Giuseppina; Lucidi, Vincenzina; Manca, Antonio; Vitullo, Pamela; Ferrara, Nicola.
Afiliação
  • Salvatore D; Cystic Fibrosis Center, Hospital San Carlo, Potenza, Italy.
  • Carnovale V; Adult Cystic Fibrosis Center, Department of Translational Medical Sciences, Federico II University of Naples, Naples, Italy.
  • Iacotucci P; Adult Cystic Fibrosis Center, Department of Translational Medical Sciences, Federico II University of Naples, Naples, Italy.
  • Braggion C; Cystic Fibrosis Center, AOU A. Meyer, Florence, Italy.
  • Castellani C; Cystic Fibrosis Centre, IRCCS Istituto Giannina Gaslini, Genoa, Italy.
  • Cimino G; Cystic Fibrosis Center, Policlinico Umberto I, Rome, Italy.
  • Colangelo C; Cystic Fibrosis Center, Hospital San Carlo, Potenza, Italy.
  • Francalanci M; Cystic Fibrosis Center, AOU A. Meyer, Florence, Italy.
  • Leonetti G; Cystic Fibrosis Center, AOU Policlinico Consorziale, Bari, Italy.
  • Lucidi V; Cystic Fibrosis Center, Ospedale Pediatrico Bambino Gesù, Rome, Italy.
  • Manca A; Cystic Fibrosis Center, Ospedale Pediatrico Bambino Gesù, Rome, Italy.
  • Vitullo P; Cystic Fibrosis Unit, Hospital G. Tatarella, Foggia, Italy.
  • Ferrara N; Cystic Fibrosis Center, Hospital San Carlo, Potenza, Italy.
Pediatr Pulmonol ; 54(9): 1398-1403, 2019 09.
Article em En | MEDLINE | ID: mdl-31237430

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Quinolonas / Regulador de Condutância Transmembrana em Fibrose Cística / Fibrose Cística / Agonistas dos Canais de Cloreto / Aminofenóis Tipo de estudo: Observational_studies / Risk_factors_studies Limite: Adolescent / Adult / Child / Female / Humans / Male / Middle aged Idioma: En Ano de publicação: 2019 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Quinolonas / Regulador de Condutância Transmembrana em Fibrose Cística / Fibrose Cística / Agonistas dos Canais de Cloreto / Aminofenóis Tipo de estudo: Observational_studies / Risk_factors_studies Limite: Adolescent / Adult / Child / Female / Humans / Male / Middle aged Idioma: En Ano de publicação: 2019 Tipo de documento: Article