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Combination molecular therapies for type 1 spinal muscular atrophy.
Harada, Yohei; Rao, Vamshi K; Arya, Kapil; Kuntz, Nancy L; DiDonato, Christine J; Napchan-Pomerantz, Galia; Agarwal, Amit; Stefans, Vikki; Katsuno, Masahisa; Veerapandiyan, Aravindhan.
Afiliação
  • Harada Y; Department of Neurology, University of Arkansas for Medical Sciences, Little Rock, Arkansas, USA.
  • Rao VK; Division of Neurology, Department of Pediatrics, Ann and Robert H. Lurie Children's Hospital of Chicago, Northwestern University Feinberg School of Medicine, Chicago, Illinois, USA.
  • Arya K; Division of Neurology, Department of Pediatrics, Arkansas Children's Hospital, University of Arkansas for Medical Sciences, Little Rock, Arkansas, USA.
  • Kuntz NL; Division of Neurology, Department of Pediatrics, Ann and Robert H. Lurie Children's Hospital of Chicago, Northwestern University Feinberg School of Medicine, Chicago, Illinois, USA.
  • DiDonato CJ; Division of Neurology, Department of Pediatrics, Ann and Robert H. Lurie Children's Hospital of Chicago, Northwestern University Feinberg School of Medicine, Chicago, Illinois, USA.
  • Napchan-Pomerantz G; Department of Pediatric Pulmonology, Joe DiMaggio Children's Hospital, Hollywood, Florida, USA.
  • Agarwal A; Division of Pulmonology, Department of Pediatrics, Arkansas Children's Hospital, University of Arkansas for Medical Sciences, Little Rock, Arkansas, USA.
  • Stefans V; Department of Pediatrics and Physical Medicine and Rehabilitation, Arkansas Children's Hospital, University of Arkansas for Medical Sciences, Little Rock, Arkansas, USA.
  • Katsuno M; Department of Neurology, Nagoya University Graduate School of Medicine, Nagoya, Japan.
  • Veerapandiyan A; Division of Neurology, Department of Pediatrics, Arkansas Children's Hospital, University of Arkansas for Medical Sciences, Little Rock, Arkansas, USA.
Muscle Nerve ; 62(4): 550-554, 2020 10.
Article em En | MEDLINE | ID: mdl-32710634

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Oligonucleotídeos / Produtos Biológicos / Proteínas Recombinantes de Fusão / Atrofias Musculares Espinais da Infância Tipo de estudo: Observational_studies Limite: Child, preschool / Female / Humans / Infant / Male Idioma: En Ano de publicação: 2020 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Oligonucleotídeos / Produtos Biológicos / Proteínas Recombinantes de Fusão / Atrofias Musculares Espinais da Infância Tipo de estudo: Observational_studies Limite: Child, preschool / Female / Humans / Infant / Male Idioma: En Ano de publicação: 2020 Tipo de documento: Article