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Pharmacokinetic and Pharmacodynamic Properties of Cemdisiran, an RNAi Therapeutic Targeting Complement Component 5, in Healthy Subjects and Patients with Paroxysmal Nocturnal Hemoglobinuria.
Badri, Prajakta; Jiang, Xuemin; Borodovsky, Anna; Najafian, Nader; Kim, Jae; Clausen, Valerie A; Goel, Varun; Habtemariam, Bahru; Robbie, Gabriel J.
Afiliação
  • Badri P; Clinical Pharmacology and Pharmacometrics, Alnylam Pharmaceuticals, 101 Main Street, Cambridge, MA, 02142, USA. pbadri@alnylam.com.
  • Jiang X; Agios Pharmaceuticals, Cambridge, MA, USA.
  • Borodovsky A; Clinical Pharmacology and Pharmacometrics, Alnylam Pharmaceuticals, 101 Main Street, Cambridge, MA, 02142, USA.
  • Najafian N; Alexion Pharmaceuticals, Boston, MA, USA.
  • Kim J; Clinical Pharmacology and Pharmacometrics, Alnylam Pharmaceuticals, 101 Main Street, Cambridge, MA, 02142, USA.
  • Clausen VA; Clinical Pharmacology and Pharmacometrics, Alnylam Pharmaceuticals, 101 Main Street, Cambridge, MA, 02142, USA.
  • Goel V; Clinical Pharmacology and Pharmacometrics, Alnylam Pharmaceuticals, 101 Main Street, Cambridge, MA, 02142, USA.
  • Habtemariam B; Clinical Pharmacology and Pharmacometrics, Alnylam Pharmaceuticals, 101 Main Street, Cambridge, MA, 02142, USA.
  • Robbie GJ; Clinical Pharmacology and Pharmacometrics, Alnylam Pharmaceuticals, 101 Main Street, Cambridge, MA, 02142, USA.
Clin Pharmacokinet ; 60(3): 365-378, 2021 03.
Article em En | MEDLINE | ID: mdl-33047216

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Complemento C5 / Hemoglobinúria Paroxística Tipo de estudo: Clinical_trials Limite: Humans Idioma: En Ano de publicação: 2021 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Complemento C5 / Hemoglobinúria Paroxística Tipo de estudo: Clinical_trials Limite: Humans Idioma: En Ano de publicação: 2021 Tipo de documento: Article