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In Vivo Gene Editing of Muscle Stem Cells with Adeno-Associated Viral Vectors in a Mouse Model of Duchenne Muscular Dystrophy.
Kwon, Jennifer B; Ettyreddy, Adarsh R; Vankara, Ashish; Bohning, Joel D; Devlin, Garth; Hauschka, Stephen D; Asokan, Aravind; Gersbach, Charles A.
Afiliação
  • Kwon JB; University Program in Genetics and Genomics, Duke University Medical Center, Durham, NC 27710, USA.
  • Ettyreddy AR; Center for Advanced Genomic Technologies, Duke University, Durham, NC 27708, USA.
  • Vankara A; Center for Advanced Genomic Technologies, Duke University, Durham, NC 27708, USA.
  • Bohning JD; Department of Biomedical Engineering, Duke University, Durham, NC 27708, USA.
  • Devlin G; Center for Advanced Genomic Technologies, Duke University, Durham, NC 27708, USA.
  • Hauschka SD; Department of Biomedical Engineering, Duke University, Durham, NC 27708, USA.
  • Asokan A; Center for Advanced Genomic Technologies, Duke University, Durham, NC 27708, USA.
  • Gersbach CA; Department of Biomedical Engineering, Duke University, Durham, NC 27708, USA.
Mol Ther Methods Clin Dev ; 19: 320-329, 2020 Dec 11.
Article em En | MEDLINE | ID: mdl-33145368

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Tipo de estudo: Risk_factors_studies Idioma: En Ano de publicação: 2020 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Tipo de estudo: Risk_factors_studies Idioma: En Ano de publicação: 2020 Tipo de documento: Article