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Evaluating the Impact of Stopping Chronic Therapies after Modulator Drug Therapy in Cystic Fibrosis: The SIMPLIFY Clinical Trial Study Design.
Mayer-Hamblett, Nicole; Nichols, David P; Odem-Davis, Katherine; Riekert, Kristin A; Sawicki, Greg S; Donaldson, Scott H; Ratjen, Felix; Konstan, Michael W; Simon, Noah; Rosenbluth, Daniel B; Retsch-Bogart, George; Clancy, John P; VanDalfsen, Jill M; Buckingham, Rachael; Gifford, Alex H.
Afiliação
  • Mayer-Hamblett N; Cystic Fibrosis Therapeutics Development Network Coordinating Center, Seattle Children's Hospital, Seattle, Washington.
  • Nichols DP; Department of Pediatrics and.
  • Odem-Davis K; Department of Biostatistics, University of Washington, Seattle, Washington.
  • Riekert KA; Cystic Fibrosis Therapeutics Development Network Coordinating Center, Seattle Children's Hospital, Seattle, Washington.
  • Sawicki GS; Department of Pediatrics and.
  • Donaldson SH; Cystic Fibrosis Therapeutics Development Network Coordinating Center, Seattle Children's Hospital, Seattle, Washington.
  • Ratjen F; Division of Pulmonary and Critical Care Medicine, Department of Medicine, School of Medicine, Johns Hopkins University, Baltimore, Maryland.
  • Konstan MW; Division of General Pediatrics and Respiratory Diseases, Boston Children's Hospital, Boston, Massachusetts.
  • Simon N; Department of Pediatrics, Harvard Medical School, Harvard University, Boston, Massachusetts.
  • Rosenbluth DB; Division of Pulmonary and Critical Care Medicine and.
  • Retsch-Bogart G; Division of Respiratory Translational Medicine Program, SickKids Research Institute, Medicine, The Hospital for Sick Children, Toronto, Ontario, Canada.
  • Clancy JP; Department of Paediatrics, University of Toronto, Toronto, Ontario, Canada.
  • VanDalfsen JM; Department of Pediatrics, Rainbow Babies and Children's Hospital and School of Medicine, Case Western Reserve University, Cleveland, Ohio.
  • Buckingham R; Cystic Fibrosis Therapeutics Development Network Coordinating Center, Seattle Children's Hospital, Seattle, Washington.
  • Gifford AH; Department of Biostatistics, University of Washington, Seattle, Washington.
Ann Am Thorac Soc ; 18(8): 1397-1405, 2021 08.
Article em En | MEDLINE | ID: mdl-33465316

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Quinolonas / Fibrose Cística Tipo de estudo: Clinical_trials / Guideline Limite: Humans Idioma: En Ano de publicação: 2021 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Quinolonas / Fibrose Cística Tipo de estudo: Clinical_trials / Guideline Limite: Humans Idioma: En Ano de publicação: 2021 Tipo de documento: Article