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Is hematopoietic stem cell transplantation a therapeutic option for mucolipidosis type II?
Ammer, Luise Sophie; Pohl, Sandra; Breyer, Sandra Rafaela; Aries, Charlotte; Denecke, Jonas; Perez, Anna; Petzoldt, Martin; Schrum, Johanna; Müller, Ingo; Muschol, Nicole Maria.
Afiliação
  • Ammer LS; Department of Pediatrics, University Medical Center Hamburg-Eppendorf, Hamburg, Germany.
  • Pohl S; International Center for Lysosomal Disorders (ICLD), University Medical Center Hamburg-Eppendorf, Hamburg, Germany.
  • Breyer SR; International Center for Lysosomal Disorders (ICLD), University Medical Center Hamburg-Eppendorf, Hamburg, Germany.
  • Aries C; Department of Osteology and Biomechanics, University Medical Center Hamburg-Eppendorf, Hamburg, Germany.
  • Denecke J; International Center for Lysosomal Disorders (ICLD), University Medical Center Hamburg-Eppendorf, Hamburg, Germany.
  • Perez A; Department of Pediatric Orthopedics, Children's Hospital Altona, Hamburg, Germany.
  • Petzoldt M; Department of Orthopedics, University Medical Center Hamburg-Eppendorf, Hamburg, Germany.
  • Schrum J; Department of Pediatrics, University Medical Center Hamburg-Eppendorf, Hamburg, Germany.
  • Müller I; International Center for Lysosomal Disorders (ICLD), University Medical Center Hamburg-Eppendorf, Hamburg, Germany.
  • Muschol NM; Department of Pediatrics, University Medical Center Hamburg-Eppendorf, Hamburg, Germany.
Mol Genet Metab Rep ; 26: 100704, 2021 Mar.
Article em En | MEDLINE | ID: mdl-33505859

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Tipo de estudo: Observational_studies Idioma: En Ano de publicação: 2021 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Tipo de estudo: Observational_studies Idioma: En Ano de publicação: 2021 Tipo de documento: Article