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Therapeutic Approaches for Duchenne Muscular Dystrophy: Old and New.
Mackenzie, Samuel J; Nicolau, Stefan; Connolly, Anne M; Mendell, Jerry R.
Afiliação
  • Mackenzie SJ; Center for Gene Therapy, Nationwide Children's Hospital, Columbus, OH; Department of Pediatrics and Neurology; The Ohio State University, Columbus, OH. Electronic address: samuel.mackenzie@nationwidechildrens.org.
  • Nicolau S; Center for Gene Therapy, Nationwide Children's Hospital, Columbus, OH.
  • Connolly AM; Center for Gene Therapy, Nationwide Children's Hospital, Columbus, OH; Department of Pediatrics and Neurology; The Ohio State University, Columbus, OH.
  • Mendell JR; Center for Gene Therapy, Nationwide Children's Hospital, Columbus, OH; Department of Pediatrics and Neurology; The Ohio State University, Columbus, OH.
Semin Pediatr Neurol ; 37: 100877, 2021 04.
Article em En | MEDLINE | ID: mdl-33892842

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Distrofia Muscular de Duchenne Limite: Humans Idioma: En Ano de publicação: 2021 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Distrofia Muscular de Duchenne Limite: Humans Idioma: En Ano de publicação: 2021 Tipo de documento: Article